日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Receptor-guided AAV Tropism Engineering via MATCH

通过 MATCH 技术进行受体引导的 AAV 嗜性工程

Graham, Nolan; Kumar, Satheesh; Rainaldi, Joseph; Yang, Seoin; Portell, Andrew; Santoso, Billy; Mali, Prashant

An engineered U7 small nuclear RNA scaffold greatly increases ADAR-mediated programmable RNA base editing

经过改造的U7小核RNA支架显著增强了ADAR介导的可编程RNA碱基编辑

Byrne, Susan M; Burleigh, Stephen M; Fragoza, Robert; Jiang, Yue; Savva, Yiannis; Pabon, Ricky; Kania, Evan; Rainaldi, Joseph; Portell, Andrew; Mali, Prashant; Briggs, Adrian W

Emerging clinical applications of ADAR based RNA editing

基于ADAR的RNA编辑技术的新兴临床应用

Rainaldi, Joseph; Mali, Prashant; Nourreddine, Sami

Transplantation of Wild-Type Hematopoietic Stem and Progenitor Cells Improves Disease Phenotypes in a Mucopolysaccharidosis IIIC Mouse Model.

移植野生型造血干细胞和祖细胞可改善粘多糖贮积症 IIIC 小鼠模型的疾病表型

Badell-Grau Rafael A, Pakravesh Kasra, Thai Kevin Eric, Son Frankie, Chen Rola, Rainaldi Joseph, Duong Kalvin, Losay Pauline, Sivakumar Anusha, Khare Veenita, Corl Alexis N, Pithia Rushil, Tran Christine, Esko Jefferey D, Cherqui Stephanie

Multiplexed Pan Soluble Ligandome Assaying via OASIS

通过 OASIS 进行多重泛可溶性配体组分析

Lee, Yi-Hung; Doctor, Yesh; Zhang, Yifan; Kumar, Satheesh; Rainaldi, Joseph; Pan, Emily; Mali, Prashant

Charting and probing the activity of ADARs in human development and cell-fate specification

绘制并探究ADARs在人类发育和细胞命运决定中的活性。

Dailamy, Amir; Lyu, Weiqi; Nourreddine, Sami; Tong, Michael; Rainaldi, Joseph; McDonald, Daniella; Panwala, Rebecca; Muotri, Alysson; Breen, Michael S; Zhang, Kun; Mali, Prashant