日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial

marstacimab预防治疗A/B型血友病伴抑制剂的疗效和安全性:来自3期BASIS试验的结果

Matino, Davide; Acharya, Suchitra S; Taylor, Carrie Turich; Sun, Pengling; Agathon, Delphine; Raje, Sangeeta; Gould, Travis; Palladino, Andrew; Mahlangu, Johnny; Lissitchkov, Toshko; Todorova, Mariya; Chan, Anthony; Carcao, Manuel; Sun, Jing; Yang, Renchi; Wu, Runhui; Jin, Chenghao; Zeng, Xiaojing; Boban, Ana; Bilic, Ernest; Frenzel, Laurent; Fung Chan, Godfrey Chi; Kong Li, Chi; Apte, Shashikant; Choraria, Nirmalkumar; Chistolini, Antonio; Marchesini, Emanuela; Peyvandi, Flora; Fujii, Teruhisa; Matsushita, Tadashi; Kaneda, Makoto; Lyu, Chuhl Joo; Park, Young Shil; Kim, SungEun; Martinez, Laura Villarreal; Adrian, Javier Morales; Wali, Yasser; Al Khabori, Murtadha; Kurtov, Igor; Alzahrani, Hazzaa; Zaher, Galila; Micic, Dragan; Miljic, Predrag; Kostic, Gordana; Vucic, Miodrag; Djurdjevic, Predrag; Hidalgo, Olga Benitez; Porras, Jose Gonzalez; Jiménez-Yuste, Víctor; Calvo Villas, Jose Manuel; Lopez Fernandez, Maria Fernanda; Albayrak, Canan; Okan, Vahap; Balkan, Can; Sahin, Fahri; Antmen, Ali; Unal, Ekrem; Visweshwar, Nathan; Sharathkumar, Anjali; Kruse-Jarres, Rebecca

Multicenter international cohort study of haploinsufficiency of A20 reveals novel genetic architecture and phenotypic evolution

一项针对A20单倍体不足的多中心国际队列研究揭示了新的遗传结构和表型演变

He, Tingyan; Wang, Jun; Carpio Tumba, Manuel; Wang, Shihao; Luo, Youyou; Chen, Jie; Li, Guomin; Shu, Zhou; Zhang, Song; Stone, Deborah L; Huang, Yanyan; Lv, Qianying; Xiong, Wen; Wang, Jinbo; Yu, Zhongxun; Cuff, Charlotte Vera; Kairis, Elizabeth; Kethri, Akuti; Towheed, Atif; Goyette, Kyr; Karri, Urekha; Wang, Jiebiao; Liu, Chen; Romeo, Tina; Alsina, Laia; Rosenberg, Daniel L; Clemente, Daniel; López-Robledillo, Juan Carlos; Rong, Zanhua; Zhao, Xue; Jiang, Lijun; Aldave-Becerra, Juan Carlos; Muñoz-Urribarri, Ana Beatriz; Oommen, Prasad Thomas; Campbell-Stokes, Priscilla; Zhu, Meifang; Liu, Peng; Guo, Li; Xu, Yiping; Yu, Zihua; Tong, Huajuan; Qiu, Xiaojian; Zhang, Yazhi; Chen, Hongbo; Zhang, Changming; Ou, Junbin; Liu, Congcong; Liu, Jinxiang; Shen, Yunyan; Cao, Jianshe; Zhang, Xinping; Yang, Kangkang; Bao, Ying; Li, Zhijuan; Cao, Jie; Duan, Yuanhui; Liu, Fujuan; Shi, Buyun; Sun, Min; Ma, Li; Chen, Yongxing; Yang, Wei; Han, Xu; Ma, Shuangyue; Luo, Jie; Gu, Weiyue; Yu, Guoliang; Shi, Weina; Zhao, Ruiqin; Sun, Lei; Li, Wenhui; An, Yunfei; Tang, Xuemei; Zhao, Xiaodong; Han, Tongxin; Ma, Jing; Li, Yan; Piao, Yurong; Sun, Fei; Zhang, Dongfeng; Yin, Meina; Zheng, Shaoling; Li, Tianwang; Niu, Huizhong; Lin, Li; Mei, Shiyue; Zhou, Fang; Yang, Sirui; Li, Danlu; Yan, Mei; Zeng, Huasong; Zeng, Ping; Zheng, Wenjie; Li, Xiaozhong; Li, Xiaolin; Liu, Yuling; Huang, Lijuan; Yu, Haiguo; Fan, Zhidan; Shen, Min; Lu, Meiping; Fang, Zhihao; Rimland, Casey Allison; Song, Hongmei; Peterson, Lance W; Yousuf Al-Nesf, Maryam Ali; Aqel, Sami; Mudawi, Dalal Sideeg; Raje, Nikita; Slowik, Voytek; Harris, Julia G; Snyder, Brenda; Scheffler-Mendoza, Selma; Yamazaki-Nakashimada, Marco Antonio; Cooper, Megan A; Lau, Yu Lung; Cetin Gedik, Kader; Wang, Wenjie; Ying, Wenjing; Hou, Jia; Zhou, Qinhua; Sun, Bijun; Sun, Jinqiao; Wang, Xiaochuan; Ombrello, Amanda K; Huang, Ying; Wu, Hai-Lin; Sun, Li; Mao, Huawei; Yu, Xiaomin; Liu, Zhihong; Aksentijevich, Ivona; Kastner, Daniel L; Schwartz, Daniella M; Yang, Jun; Zhou, Qing

Toward standardized iPSC testing: Insights from a multi-year international Quality Assessment Round

迈向标准化iPSC检测:来自多年国际质量评估轮的启示

Hägg, Alice; Wood, Rachel; Mochizuki, Ayako L; Abberton, Keren; Abranches, Elsa; Alvarez-Palomo, Belén; Baptista, Ricardo; Quintanilha Barbosa, Raiana Andrade; Barry, Jacqueline; Carvalho, Adriana Bastos; Bennaceur Griscelli, Annelise; Campos de Carvalho, Antonio Carlos; Chaker, Diana; Chang, Hong; Choi, Hye Young; Codinach, Margarita; Arán Corbella, Begoña; Cowan, Scott; Dickerson, Sarah Jane; Elwood, Ngaire; Fan, Xueling; Feyeux, Maxime; Forrester, Maddy; Gaffney, Andrew; Guilbert, Solenn M; Ha, Hye-Yeong; Hirst, Adam J; Hunter, Arwen L; Jamieson, Leanne G; Judson, Robert N; Kanemura, Yonehiro; Kasai-Brunswick, Tais Hanae; Kim, Jung-Hyun; Kim, Howard; Kintali, Manisha; Krishnan, Siddharth; Kuebler, Bernd; Lau, Chui Yu; Li, Wilson; Mack, Amanda; MacLeod, Michael R; Madrid, Marinna; Mamiya, Hiroaki; Manache-Alberici, Lucie; Mărginean, Dragoş; Mentre, Olivier; Morgan, Stefanie L; Mountford, Joanne; Munir, Humayun; Ng, Siemon H S; Ogawa, Haruna; Oh, Steve; Ohara, Hidetaka; Oono, Keiko; Park, Niall; Pereira, Lygia V; Pereira da Silva Bezerra, Izabella; Podovei, Alexandru Robert; Querol, Sergio; Raje, Jainy; Raya, Angel; Sakamoto, Satoko; Sarafian, Raquel; Schmit, Kathleen; Selvitella, Silvia; Singh, Gurbind; Smart, Matthew J K; Song, Jihwan; Stacey, Glyn; Sullivan, Stephen; Sumida, Miho; Terrenoire, Cecile; Tian, Pei; Uhlin, Elias; Vaquero, José M A; Veiga, Anna; Vicky Wang, Jar Wei; Warre-Cornish, Katherine; Wood, Jamie; Yamamoto, Atsuyo; Zhang, Gaojun; Hikichi, Takafusa; Turner, Marc; Falk, Anna

Cerebral-Protected Percutaneous Thrombectomy for Near-Occlusive LVAD Outflow Graft Thrombosis

脑保护性经皮血栓切除术治疗近乎闭塞的左心室辅助装置流出道移植物血栓形成

Chakrala, Teja S; Tanko, Toochukwu; Raje, Vikram; Charles, Lawrence; Janko, Matthew; Thompson, R Kyle; Ramadan, Ronnie; Egolum, Ugochukwu O

Cyclophosphamide mitigates non-ICANS neurotoxicities following ciltacabtagene autoleucel treatment

环磷酰胺可减轻ciltacabtagene autoleucel治疗后出现的非ICANS神经毒性

Blumenberg, Viktoria; Puliafito, Benjamin R; Graham, Charlotte E; Leick, Mark B; Chowdhury, Md Raihan; King, Maxx; Harris, Deshea L; Raje, Noopur S; Branagan, Andrew R; Yee, Andrew J; Cirstea, Diana; Gallagher, Kathleen M E; Dietrich, Jörg; Maus, Marcela V; Frigault, Matthew J

Marstacimab prophylaxis in hemophilia A/B without inhibitors: results from the phase 3 BASIS trial

在无抑制剂的A/B型血友病患者中应用马斯替单抗进行预防性治疗:来自3期BASIS试验的结果

Matino, Davide; Palladino, Andrew; Taylor, Carrie Turich; Hwang, Eunhee; Raje, Sangeeta; Nayak, Satyaprakash; McDonald, Regina; Acharya, Suchitra S; Mahlangu, Johnny; Jiménez-Yuste, Victor; Choraria, Nirmalkumar; Yang, Renchi; Li, Chi-Kong; Al-Khabori, Murtadha; Wali, Yasser; Morales Adrián, Javier; Park, Young-Shil; Zülfikar, O Bülent; Teeter, John

Immune profiling of smoldering multiple myeloma patients treated in a phase lb study of PVX-410 vaccine targeting XBP1/CD138/CS1 antigens, and citarinostat, a histone deacetylase inhibitor (HDACi) with and without lenalidomide

本研究对接受PVX-410疫苗(靶向XBP1/CD138/CS1抗原)和西他诺司他(一种组蛋白去乙酰化酶抑制剂,HDACi)联合或不联合来那度胺治疗的冒烟型多发性骨髓瘤患者进行了Ib期临床试验,并分析了接受西他诺司他治疗的冒烟型多发性骨髓瘤患者的免疫特征。

Cirstea, Diana; Shome, Rajib; Samur, Mehmet; Talluri, Srikanth; Connolly, Joseph J; Wright, Alexandra Jean; Duvallet, Emilie; Joyce, Amanda N R; Lively, Kathleen; Basinsky, Gina; Yee, Andrew J; Chase, Cristiana Costa; Malek, Ehsan; Niesvizky, Ruben; Richardson, Paul G; Raje, Noopur S

Radiation therapy to manage isolated relapse after chimeric antigen receptor T-cell therapy in multiple myeloma

放射疗法用于治疗多发性骨髓瘤嵌合抗原受体T细胞疗法后的孤立性复发

Srinivas, Surbhi; Zhu, Lin L; Raje, Noopur; Patel, Chirayu G

Engaging tribal communities for improving people's health: lessons from rural Melghat, India

动员部落社区改善人民健康:来自印度梅尔加特农村的经验教训

Ashish, Satav; Kavita, Satav; Vibhawari, Dani; Dhananjay, Raje; Shubhada, Khirwadkar; Genevie, Fernandes; Vitthal, Pande; Manik, Palaskar; Sukarai, Jambekar

Comparison of Sprague Dawley with Long Evans rats on a battery of widely used neurobehavioral tests

对 Sprague Dawley 大鼠和 Long Evans 大鼠进行一系列常用神经行为学测试的比较

Raje, Kimaya R; Williams, Michael T; Vorhees, Charles V