Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease
结合慢病毒和基因组编辑技术治疗镰状细胞病
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2021.08.019
Sophie Ramadier,Anne Chalumeau,Tristan Felix,Nadia Othman,Sherazade Aknoun,Antonio Casini,Giulia Maule,Cecile Masson,Anne De Cian,Giacomo Frati,Megane Brusson,Jean-Paul Concordet,Marina Cavazzana,Anna Cereseto,Wassim El Nemer,Mario Amendola,Benoit Wattellier,Vasco Meneghini,Annarita Miccio