日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Clinical Characteristics Associated With Variability in Biopsy Grade Severity of Liver Fibrosis in Fontan Circulation

Fontan循环中肝纤维化活检分级差异相关的临床特征

Houlihan, Taylor Hartzel; Gartenberg, Ari; Dodds, Kathryn M; Rand, Elizabeth B; Wu, Joseph; Roberts, Amy; Glatz, Andrew C; O'Byrne, Michael; Russo, Pierre; Wilkins, Benjamin; Cahill, Ann Marie; Goldberg, David J; Rychik, Jack

Postvaccination Immunogenicity Among Pediatric Solid Organ Transplant Recipients

儿童实体器官移植受者接种疫苗后的免疫原性

Feldman, Amy G; Beaty, Brenda L; Ferrolino, Jose A; Maron, Gabriela; Ali, Saira A; Bitterfeld, Leandra; Blatt, Adam; Boulware, Mary Alice; Campbell, Kathleen M; Carr, Emily; Cetin, Benhur; Chapman, Shelley; Chang, Yeh-Chung; Cunningham, Ryan; Dallas, Ronald H; Dantuluri, Keerti L; Domenick, Bryanna N; Ebel, Noelle H; Elisofon, Scott; Fawaz, Rima; Foca, Marc; Gans, Hayley A; Gopalareddy, Vani V; Gupta, Nitika A; Harmann, Katherine; Hollenbeck, Jessica; Huppler, Anna R; Jaramillo, Catalina; Kasi, Nagraj; Kerkar, Nanda; Lerret, Stacee; Lobritto, Steven J; Lopez, M James; Mavis, Alisha; Mehra, Sonia; Mohandas, Sindhu; Munoz, Flor M; Mysore, Krupa R; Ovchinsky, Nadia; Perkins, Kerrigan; Postma, Stacy; Pratscher, Lauren; Rand, Elizabeth B; Rowe, Regina K; Ruderfer, Daniel; Schultz, Danielle; Sear, Katherine; Sell, Megan L; Sharma, Tanvi S; Stoll, Janis; Turner, Jerry; Valencia Deray, Kristen G; Villarin, Dominique; Weaver, Carly; Wood, Phoebe; Woodford-Berry, Olivia; Yanni, George; Danziger-Isakov, Lara A

Condition-Specific Growth Charts for Children With Alagille Syndrome

阿拉吉尔综合征患儿的特定生长曲线图

Huysentruyt, Koen; Vandriel, Shannon M; Roelants, Mathieu; Piccoli, David A; Loomes, Kathleen M; Rand, Elizabeth B; Ebel, Noelle H; Feinstein, Jeffrey A; Jankowska, Irena; Czubkowski, Piotr; Gliwicz-Miedzinska, Dorota; Gonzales, Emmanuel M; Jacquemin, Emmanuel; Bouligand, Jérôme; Karpen, Saul J; Romero, Rene; Lin, Henry C; Fischler, Björn; Arnell, Henrik; Li, Li-Ting; Wang, Jian-She; Fawaz, Rima; Nastasio, Silvia; Kim, Kyung Mo; Oh, Seak Hee; D'Antiga, Lorenzo; Nicastro, Emanuele; Fischer, Ryan T; Siew, Susan M; Stormon, Michael; Lertudomphonwanit, Chatmanee; Hardikar, Winita; Shankar, Sahana; Squires, James E; Sundaram, Shikha S; Larson-Nath, Catherine; Kelly, Deirdre A; Hartley, Jane; Bulut, Pinar; Jensen, M Kyle; Jaramillo, Catalina; Roberts, Amin J; Evans, Helen M; Sokal, Étienne M; Demaret, Tanguy; Verkade, Henkjan J; Thompson, Richard J; Hansen, Bettina E; Cole, Tim J; Kamath, Binita M; Debray, Dominique; Lacaille, Florence; Brecelj, Jernej; El-Koofy, Nehal M; Elmonem, Mohamed A; Lee, Way Seah; Sanchez, Maria Camila; Cavalieri, Maria Lorena; Hajinicolaou, Christina; Schwarz, Kathleen B; Carvalho, Elisa; Rock, Nathalie; Karnsakul, Wikrom; Quiros-Tejeira, Ruben E; Alam, Seema; Nebbia, Gabriella; Mozer-Glassberg, Yael; Valentino, Pamela L; Santos-Silva, Ermelinda; Önal, Zerrin; Dezsofi-Gottl, Antal; Melere, Melina; Legarda Tamara, María; Eshun, John; Zellos, Aglaia; Indolfi, Giuseppe; Rogalidou, Maria; Blondet, Niviann; Luigi Calvo, Pier; Beretta, Marisa; Zizzo, Andréanne N; Arikan, Cigdem; Kasahara, Mureo; Kerkar, Nanda; Aqul, Amal A; Wolters, Victorien M; Borges Pinto, Raquel; Quintero Bernabeu, Jesus; Garcia, Jennifer; Wiecek, Sabina; Tzivinikos, Christos; Mujawar, Quais; Jimenez-Rivera, Carolina; Molera Busoms, Cristina; Gonçalves, Cristina; Bujanda, Luis

Elevated Serum Bile Acids Predict Poor Liver Outcomes in Children With Alagille Syndrome: Results From the GALA Study Group

血清胆汁酸水平升高预示阿拉吉勒综合征患儿肝脏预后不良:GALA研究组的结果

Perez, Carla Fiorella Murillo; Vandriel, Shannon M; Gonzales, Emmanuel M; Wang, Jian-She; Li, Li-Ting; She, Huiyu; Jankowska, Irena; Czubkowski, Piotr; Gliwicz-Miedzińska, Dorota; Jacquemin, Emmanuel; Bouligand, Jérôme; D'Antiga, Lorenzo; Nicastro, Emanuele; Fischler, Björn; Arnell, Henrik; Siew, Susan M; Stormon, Michael; Loomes, Kathleen M; Piccoli, David A; Rand, Elizabeth B; Squires, James E; Karpen, Saul J; Romero, Rene; Kasahara, Mureo; Önal, Zerrin; Sokal, Étienne; Demaret, Tanguy; Wiecek, Sabina; Lacaille, Florence; Debray, Dominique; Hardikar, Winita; Shankar, Sahana; Valentino, Pamela L; Sundaram, Shikha S; Ebel, Noelle H; Feinstein, Jeffrey A; Waisbourd-Zinman, Orith; Lin, Henry C; Rock, Nathalie; Verkade, Henkjan J; Jensen, M Kyle; Jaramillo, Catalina; Kim, Kyung Mo; Oh, Seak Hee; Brecemiclj, Jernej; Alam, Seema; Indolfi, Giuseppe; Blondet, Niviann; Fawaz, Rima; Nastasio, Silvia; Calvo, Pier Luigi; Nebbia, Gabriella; Arikan, Cigdem; Larson-Nath, Catherine; Zizzo, Andréanne N; Sandahl, Thomas Damgaard; Tzivinikos, Christos; El-Koofy, Nehal M; Elmonem, Mohamed A; Aqul, Amal A; Karnsakul, Wikrom; Bulut, Pinar; Kerkar, Nanda; Wolters, Victorien M; Roberts, Amin J; Evans, Helen M; Sanchez, Maria Camila; Cavalieri, Maria Lorena; Kelly, Deirdre A; Hartley, Jane; Lee, Way Seah; Hajinicolaou, Christina; Lertudomphonwanit, Chatmanee; Fischer, Ryan T; Bernabeu, Jesus Quintero; Quiros-Tejeira, Ruben E; Ferreira, Cristina Targa; Carvalho, Elisa; Eshun, John; Zellos, Aglaia; Dezsőfi, Antal; Pinto, Raquel Borges; Schwarz, Kathleen; Rogalidou, Maria; Garcia, Jennifer; Tamara, María Legarda; Beretta, Marisa; Mujawar, Quais; Santos-Silva, Ermelinda; Busoms, Cristina Molera; Lurz, Eberhard; Gonçalves, Cristina; Jimenez-Rivera, Carolina; Banales, Jesus M; Thompson, Richard J; Hansen, Bettina E; Kamath, Binita M

Liver Transplant From a Deceased Donor With Cystinosis: A Case Report

一例胱氨酸病患者遗体肝移植病例报告

Taj, Raeda; Ng, Kim; Cuddapah, Sanmati R; Rand, Elizabeth B; Bleicher, Melissa; Amaral, Sandra; Hoteit, Maarouf A; Reddy, Rajendar K; Feyssa, Eyob; Furth, Emma E; Olthoff, Kim M; Abu-Gazala, Samir; Levine, Matthew H; Vyas, Frederick; Abt, Peter L

Treatment of intractable pruritus with maralixibat in patients with Alagille syndrome before and after reversal of biliary diversion

在胆道改道术逆转前后,使用马拉利西巴治疗阿拉吉勒综合征患者的顽固性瘙痒

Nwachukwu, Chiamaka; LeVine, David; Himes, Ryan; Seal, John; Domenick, Bryanna; Rand, Elizabeth B; Diamond, Tamir

Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA

与来自 GALA 的真实世界队列相比,接受 maralixibat 治疗的 Alagille 综合征患者的无事件生存期

Hansen, Bettina E; Vandriel, Shannon M; Vig, Pamela; Garner, Will; Mogul, Douglas B; Loomes, Kathleen M; Piccoli, David A; Rand, Elizabeth B; Jankowska, Irena; Czubkowski, Piotr; Gliwicz-Miedzińska, Dorota; Gonzales, Emmanuel M; Jacquemin, Emmanuel; Bouligand, Jérôme; D'Antiga, Lorenzo; Nicastro, Emanuele; Arnell, Henrik; Fischler, Björn; Sokal, Étienne; Demaret, Tanguy; Siew, Susan; Stormon, Michael; Karpen, Saul J; Romero, Rene; Ebel, Noelle H; Feinstein, Jeffrey A; Roberts, Amin J; Evans, Helen M; Sundaram, Shikha S; Chaidez, Alexander; Hardikar, Winita; Shankar, Sahana; Fischer, Ryan T; Lacaille, Florence; Debray, Dominique; Lin, Henry C; Jensen, M Kyle; Jaramillo, Catalina; Karthikeyan, Palaniswamy; Indolfi, Giuseppe; Verkade, Henkjan J; Larson-Nath, Catherine; Quiros-Tejeira, Ruben E; Valentino, Pamela L; Rogalidou, Maria; Dezsőfi, Antal; Squires, James E; Schwarz, Kathleen; Calvo, Pier Luigi; Bernabeu, Jesus Quintero; Zizzo, Andréanne N; Nebbia, Gabriella; Bulut, Pinar; Santos-Silva, Ermelinda; Fawaz, Rima; Nastasio, Silvia; Karnsakul, Wikrom; Tamara, María Legarda; Busoms, Cristina Molera; Kelly, Deirdre A; Sandahl, Thomas Damgaard; Jimenez-Rivera, Carolina; Banales, Jesus M; Mujawar, Quais; Li, Li-Ting; She, Huiyu; Wang, Jian-She; Kim, Kyung Mo; Oh, Seak Hee; Sanchez, Maria Camila; Cavalieri, Maria Lorena; Lee, Way Seah; Hajinicolaou, Christina; Lertudomphonwanit, Chatmanee; Waisbourd-Zinman, Orith; Arikan, Cigdem; Alam, Seema; Carvalho, Elisa; Melere, Melina; Eshun, John; Önal, Zerrin; Desai, Dev M; Wiecek, Sabina; Pinto, Raquel Borges; Wolters, Victorien M; Garcia, Jennifer; Beretta, Marisa; Kerkar, Nanda; Brecelj, Jernej; Rock, Nathalie; Lurz, Eberhard; Blondet, Niviann; Shah, Uzma; Thompson, Richard J; Kamath, Binita M

Novel insights into the phenotypic spectrum and pathogenesis of Hardikar syndrome.

对哈迪卡综合征的表型谱和发病机制的新见解

Strong Alanna, March Michael E, Cardinale Christopher J, Liu Yichuan, Battig Mark R, Finoti Livia Sertori, Matsuoka Leticia S, Watson Deborah, Sridhar Sindura, Jarrett James F, Cannon India, Li Dong, Bhoj Elizabeth, Zackai Elaine H, Rand Elizabeth B, Wenger Tara, Lerman Bruce B, Shikany Amy, Weaver K Nicole, Hakonarson Hakon

Safety and Immunogenicity of Live Viral Vaccines in a Multicenter Cohort of Pediatric Transplant Recipients

活病毒疫苗在多中心儿科移植受者队列中的安全性和免疫原性

Feldman, Amy G; Beaty, Brenda L; Ferrolino, Jose A; Maron, Gabriela; Weidner, Hillary K; Ali, Saira A; Bitterfeld, Leandra; Boulware, Mary Alice; Campbell, Kathleen M; Carr, Emily; Chapman, Shelley; Chang, Yeh-Chung; Cunningham, Ryan; Dallas, Ronald H; Dantuluri, Keerti L; Domenick, Bryanna N; Ebel, Noelle H; Elisofon, Scott; Fawaz, Rima; Foca, Marc; Gans, Hayley A; Gopalareddy, Vani V; Gu, Cindy; Gupta, Nitika A; Harmann, Katherine; Hollenbeck, Jessica; Huppler, Anna R; Jaramillo, Catalina; Kasi, Nagraj; Kerkar, Nanda; Lerret, Stacee; Lobritto, Steven J; Lopez, Maclovio J; Marini, Elizabeth; Mavis, Alisha; Mehra, Sonia; Moats, Lynnette; Mohandas, Sindhu; Munoz, Flor M; Mysore, Krupa R; Onsan, Ceren; Ovchinsky, Nadia; Perkins, Kerrigan; Postma, Stacy; Pratscher, Lauren; Rand, Elizabeth B; Rowe, Regina K; Schultz, Danielle; Sear, Katherine; Sell, Megan L; Sharma, Tanvi; Stoll, Janis; Vang, Mychoua; Villarin, Dominique; Weaver, Carly; Wood, Phoebe; Woodford-Berry, Olivia; Yanni, George; Danziger-Isakov, Lara A

Liver Biopsy Leads to Serendipitous Diagnosis of Glycogen Storage Disease Type IX in a Patient With Fontan-Associated Liver Disease

肝活检意外发现一名接受过Fontan手术的肝病患者患有IX型糖原贮积症

Hyer, Erin; Alexander, Caitlin; Rand, Elizabeth B; Diamond, Tamir