日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report

造血干细胞移植治疗威斯科特-奥尔德里奇综合征:PIDTC报告

Alexander, Jessie L; Dávila Saldaña, Blachy J; Brazauskas, Ruta; Dammalapati, Sravya Gethika; Griffith, Linda M; Shah, Ami J; Shimano, Kristin A; Ochs, Hans D; Bleesing, Jack J; Ebens, Christen L; Kapadia, Malika; Bauchat, Andrea; Kapoor, Neena; Oved, Joseph H; Eissa, Hesham; Lust, Hannah; Keller, Michael D; Haines, Hilary; Chandrakasan, Shanmuganathan; Talano, Julie-An; Rayes, Ahmad; Madden, Lisa; Shereck, Evan; Miller, Holly K; Satter, Lisa Forbes; Martinez, Caridad; Rozmus, Jacob; Bednarski, Jeffrey J; Yu, Lolie C; Chellapandian, Deepakbabu; Aquino, Victor M; Knutsen, Alan; Chong, Hey; Chopek, Ashley; Gillio, Alfred P; Joshi, Avni; Rangarajan, Hemalatha; Moore, Theodore B; Andolina, Jeffrey R; DeSantes, Kenneth B; Vander Lugt, Mark; Prockop, Susan E; Shyr, David C; Sullivan, Kathleen E; Parikh, Suhag; Weinacht, Katja G; Torgerson, Troy R; Marsh, Rebecca; Dvorak, Christopher C; Chan, Alice Y; Haddad, Elie; Heimall, Jennifer R; Pulsipher, Michael A; Leiding, Jennifer W; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Rawlings, David J; Cowan, Morton J; Petrovic, Aleksandra; Pai, Sung-Yun; Burroughs, Lauri M

Treatment of canine hemophilia A via intraosseous delivery of a platelet-specific factor VIII-lentiviral vector

通过骨内注射血小板特异性因子VIII慢病毒载体治疗犬血友病A

Rementer, Cameron W; Li, Chong; Nichols, Timothy C; Cai, Xiaohe; Joo, Julia; Wang, Xuefeng; Kloos, Mark; George, Nneka; Chao, Ting-Yen; Xu, Yuanyi; Poncz, Mortimer; Ochs, Hans D; Rawlings, David J; Miao, Carol H

Targeting human plasma cells using regulated BCMA CAR T cells eliminates circulating antibodies in humanized mice.

利用调控的BCMA CAR T细胞靶向人类浆细胞,可消除人源化小鼠体内的循环抗体

Honaker Yuchi, Gruber David, Jacobs Chester, Yu-Hong Cheng Rene, Patel Shivani, Galvan Christopher Zavala, Khan Iram F, Zhou Kevin, Sommer Karen, Astrakhan Alexander, Cook Peter J, James Richard G, Rawlings David J

Reduced Function of the Adaptor SH2B3 Promotes T1D via Altered Cytokine-Regulated, T-Cell-Intrinsic Immune Tolerance

衔接蛋白SH2B3功能降低通过改变细胞因子调节的T细胞固有免疫耐受性促进1型糖尿病的发生

Watson, Taylor K; Rosen, Aaron B I; Drow, Travis; Medjo, Jacob A; MacQuivey, Matthew A; Ge, Yan; Liggitt, H Denny; Grosvenor, Dane A; Dill-McFarland, Kimberly A; Altman, Matthew C; Concannon, Patrick J; Buckner, Jane H; Rawlings, David J; Allenspach, Eric J

Hypomorphic RAG2 Deficiency Promotes Selection of Self-Reactive B Cells

RAG2功能减退缺陷促进自身反应性B细胞的选择

Thouvenel, Christopher D; Tipton, Christopher M; Yamazaki, Yasuhiro; Zhang, Ting-Ting; Rylaarsdam, Stacey; Hom, Jennifer R; Snead, Catherine; Zhu, Chengsong; Li, Quan-Zhen; Lee, Yu Nee; Kawai, Tomoki; Haque, Neshatul; Zimmermann, Michael T; Ponnan, Sivasankaran Munusamy; Jackson, Shaun W; James, Rich G; Sanz, Ignacio; Notarangelo, Luigi D; Torgerson, Troy R; Ochs, Hans D; Rawlings, David J; Allenspach, Eric J

PI3Kdelta-driven expansion of regulatory B cells impairs protective immune responses to Trypanosoma congolense parasite infection

PI3Kδ驱动的调节性B细胞扩增会削弱对刚果锥虫寄生虫感染的保护性免疫反应。

Olayinka-Adefemi, Folayemi; Wu, Xun; Hou, Sen; Sabzevary-Ghahfarokhi, Milad; Wray-Dutra, Michelle N; Rawlings, David J; Uzonna, Jude; Marshall, Aaron J

HLA-A2 CAR/IL-2-CISC engineered Treg display robust in vitro and in vivo antigen-specific regulatory function

HLA-A2 CAR/IL-2-CISC工程化Treg细胞在体外和体内均表现出强大的抗原特异性调节功能。

Tripathi, Subhash K; Grimm, Annaiz; Dahl, Noelle P; Honaker, Yuchi; Knebusch, Parker; Chen, Yu; Cook, Peter J; Rawlings, David J

Humanized mice enable in vivo evaluation of engineered plasma cell biology and therapeutic function

人源化小鼠能够对工程化浆细胞生物学和治疗功能进行体内评估。

Hill, Tyler F; Helmers, Anna E; Cheng, Rene Yu-Hong; Singh, Swati; Homad, Leah J; Narvekar, Parnal; Asher, Gregory D; Camp, Nathan D; Suchland, Emma R; Ott, Andee R; Hale, Malika; Thouvenel, Chris D; Stoffers, Claire M; Lachkar, Stefan; McGuire, Andrew T; Rawlings, David J; James, Richard G

Human plasma cells engineered to secrete bispecifics drive effective in vivo leukemia killing.

经基因工程改造可分泌双特异性抗体的人类浆细胞可有效杀灭体内白血病细胞

Hill Tyler F, Narvekar Parnal, Asher Gregory D, Edelstein Jasmine N, Camp Nathan D, Grimm Annaiz, Thomas Kerri R, Leiken Michael D, Molloy Katherine M, Cook Peter J, Arlauckas Sean P, Morgan Richard A, Tasian Sarah K, Rawlings David J, James Richard G

The IFIH1-A946T risk variant promotes diabetes in a sex-dependent manner

IFIH1-A946T风险变异以性别依赖的方式促进糖尿病的发生。

Stock, Amanda J; Gonzalez Paredes, Pierina; de Almeida, Luciana Previato; Kosanke, Stanley D; Chetlur, Srinivaas; Budde, Hannah; Wakenight, Paul; Zwingman, Theresa A; Rosen, Aaron B I; Allenspach, Eric J; Millen, Kathleen J; Buckner, Jane H; Rawlings, David J; Gorman, Jacquelyn A