日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intracerebroventricular B7-H3-targeting CAR T cells for diffuse intrinsic pontine glioma: a phase 1 trial

脑室内注射靶向B7-H3的CAR-T细胞治疗弥漫性内生性桥脑胶质瘤:一项I期试验

Vitanza, Nicholas A; Ronsley, Rebecca; Choe, Michelle; Seidel, Kristy; Huang, Wenjun; Rawlings-Rhea, Stephanie D; Beam, Madison; Steinmetzer, Leonel; Wilson, Ashley L; Brown, Christopher; Beebe, Adam; Lindgren, Catherine; Gustafson, Joshua A; Wein, Amy; Holtzclaw, Susan; Hoeppner, Corrine; Goldstein, Hannah E; Browd, Samuel R; Hauptman, Jason S; Lee, Amy; Ojemann, Jeffrey G; Crotty, Erin E; Leary, Sarah E S; Perez, Francisco A; Wright, Jason N; Alonso, Marta M; Dun, Matthew D; Foster, Jessica B; Hurst, Diana; Kong, Ada; Thomsen, Alison; Orentas, Rimas J; Albert, Catherine M; Pinto, Navin; Annesley, Colleen; Gardner, Rebecca A; Ho, On; Pattabhi, Sowmya; Gust, Juliane; Wendler, Jason P; Park, Julie R; Jensen, Michael C

Outcomes of PLAT-02 and PLAT-03: evaluating CD19 CAR T-cell therapy and CD19-expressing T-APC support in pediatric B-ALL

PLAT-02 和 PLAT-03 研究结果:评估 CD19 CAR T 细胞疗法和表达 CD19 的 T-APC 支持治疗儿童 B 细胞急性淋巴细胞白血病 (B-ALL) 的疗效

Annesley, Colleen; Seidel, Kristy; Wu, Qian; Summers, Corinne; Wayne, Alan S; Pulsipher, Michael A; Agrawal, Anurag K; Brown, Chris T; Mgebroff, Stephanie; Lindgren, Catherine; Rawlings-Rhea, Stephanie; Huang, Wenjun; Wilson, Ashley L; Jensen, Michael C; Park, Julie R; Gardner, Rebecca A

Locoregional infusion of EGFR806-CAR T cells for recurrent or refractory pediatric CNS tumors: Results of the completed BrainChild02 phase 1 clinical trial

局部区域输注EGFR806-CAR T细胞治疗复发性或难治性儿童中枢神经系统肿瘤:已完成的BrainChild02 I期临床试验结果

Gust, Juliane; Cole, Bonnie L; Ronsley, Rebecca; Wilson, Ashley L; Seidel, Kristy; Wendler, Jason; Pattabhi, Sowmya; Brown, Christopher; Rawlings-Rhea, Stephanie D; Shtanukhina, Nadezhda; Browd, Samuel R; Hauptman, Jason S; Lee, Amy; Ojemann, Jeffrey G; Crotty, Erin E; Leary, Sarah E S; Perez, Francisco A; Wright, Jason N; Albert, Catherine M; Pinto, Navin; Gardner, Rebecca A; Vitanza, Nicholas A; Jensen, Michael C; Park, Julie R

Intraventricular B7-H3 CAR T Cells for Diffuse Intrinsic Pontine Glioma: Preliminary First-in-Human Bioactivity and Safety

脑室内注射B7-H3 CAR T细胞治疗弥漫性内生性脑桥胶质瘤:初步人体生物活性和安全性研究

Nicholas A Vitanza ,Ashley L Wilson ,Wenjun Huang ,Kristy Seidel ,Christopher Brown ,Joshua A Gustafson ,Jason K Yokoyama ,Adam J Johnson ,Blake A Baxter ,Ryan W Koning ,Aquene N Reid ,Michael Meechan ,Matthew C Biery ,Carrie Myers ,Stephanie D Rawlings-Rhea ,Catherine M Albert ,Samuel R Browd ,Jason S Hauptman ,Amy Lee ,Jeffrey G Ojemann ,Michael E Berens ,Matthew D Dun ,Jessica B Foster ,Erin E Crotty ,Sarah E S Leary ,Bonnie L Cole ,Francisco A Perez ,Jason N Wright ,Rimas J Orentas ,Tony Chour ,Evan W Newell ,Jeffrey R Whiteaker ,Lei Zhao ,Amanda G Paulovich ,Navin Pinto ,Juliane Gust ,Rebecca A Gardner ,Michael C Jensen # ,Julie R Park #

GFAP and NfL increase during neurotoxicity from high baseline levels in pediatric CD19-CAR T-cell patients

在儿童CD19-CAR T细胞患者中,神经毒性期间GFAP和NfL水平从较高的基线水平升高。

Gust, Juliane; Rawlings-Rhea, Stephanie D; Wilson, Ashley L; Tulberg, Niklas M; Sherman, Amber L; Seidel, Kristy D; Wu, Qian Vicky; Park, Julie R; Gardner, Rebecca A; Annesley, Colleen E

Modified Manufacturing Process Modulates CD19CAR T-cell Engraftment Fitness and Leukemia-Free Survival in Pediatric and Young Adult Subjects

改进的生产工艺可调节CD19CAR T细胞在儿童和青少年受试者中的植入效果和无白血病生存期

Francesco Ceppi # ,Ashley L Wilson # ,Colleen Annesley ,Gabriella R Kimmerly ,Corinne Summers ,Adam Brand ,Kristy Seidel ,Qian Vicky Wu ,Adam Beebe ,Christopher Brown ,Stephanie Mgebroff ,Catherine Lindgren ,Stephanie D Rawlings-Rhea ,Wenjun Huang ,Michael A Pulsipher ,Alan S Wayne ,Julie R Park ,Michael C Jensen ,Rebecca A Gardner

Alignment of practices for data harmonization across multi-center cell therapy trials: a report from the Consortium for Pediatric Cellular Immunotherapy

多中心细胞治疗试验数据协调实践的统一:儿科细胞免疫治疗联盟的报告

Abdel-Azim, Hisham; Dave, Hema; Jordan, Kimberly; Rawlings-Rhea, Stephanie; Luong, Annie; Wilson, Ashley L

Locoregional infusion of HER2-specific CAR T cells in children and young adults with recurrent or refractory CNS tumors: an interim analysis

HER2 特异性 CAR-T 细胞局部区域输注在患有复发性或难治性中枢神经系统肿瘤的儿童和年轻人中的效果:中期分析

Nicholas A Vitanza, Adam J Johnson, Ashley L Wilson, Christopher Brown, Jason K Yokoyama, Annette Künkele, Cindy A Chang, Stephanie Rawlings-Rhea, Wenjun Huang, Kristy Seidel, Catherine M Albert, Navin Pinto, Juliane Gust, Laura S Finn, Jeffrey G Ojemann, Jason Wright, Rimas J Orentas, Michael Baldw

CD19 CAR T cell product and disease attributes predict leukemia remission durability

CD19 CAR T 细胞产品和疾病特征可预测白血病缓解的持久性。

Olivia C Finney, Hannah M Brakke, Stephanie Rawlings-Rhea, Roxana Hicks, Danielle Doolittle, Marisa Lopez, Robert B Futrell, Rimas J Orentas, Daniel Li, Rebecca A Gardner, Michael C Jensen

Glial injury in neurotoxicity after pediatric CD19-directed chimeric antigen receptor T cell therapy

儿童CD19靶向嵌合抗原受体T细胞疗法后神经毒性中的胶质细胞损伤

Gust, Juliane; Finney, Olivia C; Li, Daniel; Brakke, Hannah M; Hicks, Roxana M; Futrell, Robert B; Gamble, Danielle N; Rawlings-Rhea, Stephanie D; Khalatbari, Hedieh K; Ishak, Gisele E; Duncan, Virginia E; Hevner, Robert F; Jensen, Michael C; Park, Julie R; Gardner, Rebecca A