日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RAS pathway targeted therapy in patients with DICER1-associated sarcomas

RAS通路靶向治疗在DICER1相关肉瘤患者中的应用

Zhang, Lindy; Mallinger, Paige H R; Zhou, Serena; Makri, Stavriani C; Gross, John M; Lucas, Calixto-Hope G; Zou, Ying S; Mize, William; Olson, Damon R; Munnikhuysen, Senna R; Rawwas, Jawhar; Messinger, Yoav; Chen, Kenneth S; Schultz, Kris Ann P; Pratilas, Christine A

Molecular-guided therapy for the treatment of patients with relapsed and refractory childhood cancers: a Beat Childhood Cancer Research Consortium trial

分子靶向治疗复发难治性儿童癌症患者:一项由“战胜儿童癌症研究联盟”开展的试验

Sholler, Giselle L Saulnier; Bergendahl, Genevieve; Lewis, Elizabeth C; Kraveka, Jacqueline; Ferguson, William; Nagulapally, Abhinav B; Dykema, Karl; Brown, Valerie I; Isakoff, Michael S; Junewick, Joseph; Mitchell, Deanna; Rawwas, Jawhar; Roberts, William; Eslin, Don; Oesterheld, Javier; Wada, Randal K; Pastakia, Devang; Harrod, Virginia; Ginn, Kevin; Saab, Raya; Bielamowicz, Kevin; Glover, Jason; Chang, Eugenia; Hanna, Gina K; Enriquez, Daniel; Izatt, Tyler; Halperin, Rebecca F; Moore, Abigail; Byron, Sara A; Hendricks, William P D; Trent, Jeffrey M

A pilot study of genomic-guided induction therapy followed by immunotherapy with difluoromethylornithine maintenance for high-risk neuroblastoma

一项针对高危神经母细胞瘤的基因组指导诱导治疗后序贯二氟甲基鸟氨酸维持免疫治疗的试点研究

Kraveka, Jacqueline M; Lewis, Elizabeth C; Bergendahl, Genevieve; Ferguson, William; Oesterheld, Javier; Kim, Elizabeth; Nagulapally, Abhinav B; Dykema, Karl J; Brown, Valerie I; Roberts, William D; Mitchell, Deanna; Eslin, Don; Hanson, Derek; Isakoff, Michael S; Wada, Randal K; Harrod, Virginia L; Rawwas, Jawhar; Hanna, Gina; Hendricks, William P D; Byron, Sara A; Snuderl, Matija; Serrano, Jonathan; Trent, Jeffrey M; Saulnier Sholler, Giselle L

Genomic and Transcriptomic Analysis of Relapsed and Refractory Childhood Solid Tumors Reveals a Diverse Molecular Landscape and Mechanisms of Immune Evasion

复发和难治性儿童实体瘤的基因组和转录组分析揭示了其多样化的分子图谱和免疫逃逸机制

Byron, Sara A; Hendricks, William P D; Nagulapally, Abhinav B; Kraveka, Jacqueline M; Ferguson, William S; Brown, Valerie I; Eslin, Don E; Mitchell, Deanna; Cornelius, Albert; Roberts, William; Isakoff, Michael S; Oesterheld, Javier E; Wada, Randal K; Rawwas, Jawhar; Neville, Kathleen; Zage, Peter E; Harrod, Virginia L; Bergendahl, Genevieve; VanSickle, Elizabeth; Dykema, Karl; Bond, Jeffrey; Chou, Hsien-Chao; Wei, Jun S; Wen, Xinyu; Reardon, Hue V; Roos, Alison; Nasser, Sara; Izatt, Tyler; Enriquez, Daniel; Hegde, Apurva M; Cisneros, Faith; Christofferson, Austin; Turner, Bryce; Szelinger, Szabolcs; Keats, Jonathan J; Halperin, Rebecca F; Khan, Javed; Saulnier Sholler, Giselle L; Trent, Jeffrey M

Gene therapy for spinal muscular atrophy: the Qatari experience

脊髓性肌萎缩症的基因疗法:卡塔尔的经验

Ali, Hossamaldein Gaber; Ibrahim, Khalid; Elsaid, Mahmoud Fawzi; Mohamed, Reem Babiker; Abeidah, Mahmoud I A; Al Rawwas, Azhar Othman; Elshafey, Khaled; Almulla, Hajer; El-Akouri, Karen; Almulla, Mariam; Othman, Amna; Musa, Sara; Al-Mesaifri, Fatma; Ali, Rehab; Shahbeck, Noora; Al-Mureikhi, Mariam; Alsulaiman, Reem; Alkaabi, Saad; Ben-Omran, Tawfeg

FET(EWSR1)-TFCP2 Rhabdomyosarcoma: An Additional Example of this Aggressive Variant with Predilection for the Gnathic Bones

FET(EWSR1)-TFCP2 横纹肌肉瘤:又一例好发于颌骨的侵袭性变异型

Koutlas, Ioannis G; Olson, Damon R; Rawwas, Jawhar

Agricultural workers in meatpacking plants presenting to an emergency department with suspected COVID-19 infection are disproportionately Black and Hispanic

在肉类加工厂因疑似感染新冠病毒而前往急诊室就诊的农业工人中,黑人和西班牙裔的比例过高。

House, Hans R; Vakkalanka, J Priyanka; Behrens, Nathan G; De Haan, Jessica; Halbur, Christopher R; Harrington, Elaine M; Patel, Pooja H; Rawwas, Lulua; Camargo, Carlos A Jr; Kline, Jeffrey A

A subset analysis of a phase II trial evaluating the use of DFMO as maintenance therapy for high-risk neuroblastoma

一项评估DFMO作为高危神经母细胞瘤维持治疗的II期试验的子集分析

Lewis, Elizabeth C; Kraveka, Jacqueline M; Ferguson, William; Eslin, Don; Brown, Valerie I; Bergendahl, Genevieve; Roberts, William; Wada, Randal K; Oesterheld, Javier; Mitchell, Deanna; Foley, Jessica; Zage, Peter; Rawwas, Jawhar; Rich, Maria; Lorenzi, Elizabeth; Broglio, Kristine; Berry, Donald; Saulnier Sholler, Giselle L

Segmental Chromosomal Aberrations in Localized Neuroblastoma Can be Detected in Formalin-Fixed Paraffin-Embedded Tissue Samples and Are Associated With Recurrence

局限性神经母细胞瘤的节段性染色体畸变可在福尔马林固定石蜡包埋组织样本中检测到,且与复发相关。

Pinto, Navin; Mayfield, Jodi R; Raca, Gordana; Applebaum, Mark A; Chlenski, Alexandre; Sukhanova, Madina; Bagatell, Rochelle; Irwin, Meredith S; Little, Anthony; Rawwas, Jawhar; Gosiengfiao, Yasmin; Delattre, Olivier; Janoueix-Lerosey, Isabelle; Lapouble, Eve; Schleiermacher, Gudrun; Cohn, Susan L