日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Functional footprinting of regulatory DNA

调控DNA的功能足迹分析

Vierstra, Jeff; Reik, Andreas; Chang, Kai-Hsin; Stehling-Sun, Sandra; Zhou, Yuanyue; Hinkley, Sarah J; Paschon, David E; Zhang, Lei; Psatha, Nikoletta; Bendana, Yuri R; O'Neil, Colleen M; Song, Alexander H; Mich, Andrea K; Liu, Pei-Qi; Lee, Gary; Bauer, Daniel E; Holmes, Michael C; Orkin, Stuart H; Papayannopoulou, Thalia; Stamatoyannopoulos, George; Rebar, Edward J; Gregory, Philip D; Urnov, Fyodor D; Stamatoyannopoulos, John A

Human intestinal tissue with adult stem cell properties derived from pluripotent stem cells

源自多能干细胞的具有成体干细胞特性的人类肠道组织

Forster, Ryan; Chiba, Kunitoshi; Schaeffer, Lorian; Regalado, Samuel G; Lai, Christine S; Gao, Qing; Kiani, Samira; Farin, Henner F; Clevers, Hans; Cost, Gregory J; Chan, Andy; Rebar, Edward J; Urnov, Fyodor D; Gregory, Philip D; Pachter, Lior; Jaenisch, Rudolf; Hockemeyer, Dirk

Heterochromatin Dynamics during the Differentiation Process Revealed by the DNA Methylation Reporter Mouse, MethylRO

DNA甲基化报告基因小鼠MethylRO揭示了分化过程中异染色质的动态变化

Sadek, Hesham A; Martin, James F; Takeuchi, Jun K; Leor, Jonathan; Nie, Yu; Giacca, Mauro; Lee, Richard T; Forster, Ryan; Chiba, Kunitoshi; Schaeffer, Lorian; Regalado, Samuel G; Lai, Christine S; Gao, Qing; Kiani, Samira; Farin, Henner F; Clevers, Hans; Cost, Gregory J; Chan, Andy; Rebar, Edward J; Urnov, Fyodor D; Gregory, Philip D; Pachter, Lior; Jaenisch, Rudolf; Hockemeyer, Dirk; Yu, Diana Xuan; Di Giorgio, Francesco Paolo; Yao, Jun; Marchetto, Maria Carolina; Brennand, Kristen; Wright, Rebecca; Mei, Arianna; Mchenry, Lauren; Lisuk, David; Grasmick, Jaeson Michael; Silberman, Pedro; Silberman, Giovanna; Jappelli, Roberto; Gage, Fred H; Ueda, Jun; Maehara, Kazumitsu; Mashiko, Daisuke; Ichinose, Takako; Yao, Tatsuma; Hori, Mayuko; Sato, Yuko; Kimura, Hiroshi; Ohkawa, Yasuyuki; Yamagata, Kazuo

Toward eliminating HLA class I expression to generate universal cells from allogeneic donors

旨在消除HLA I类分子的表达,从而从同种异体供体中生成通用细胞

Torikai, Hiroki; Reik, Andreas; Soldner, Frank; Warren, Edus H; Yuen, Carrie; Zhou, Yuanyue; Crossland, Denise L; Huls, Helen; Littman, Nicholas; Zhang, Ziying; Tykodi, Scott S; Kebriaei, Partow; Lee, Dean A; Miller, Jeffrey C; Rebar, Edward J; Holmes, Michael C; Jaenisch, Rudolf; Champlin, Richard E; Gregory, Philip D; Cooper, Laurence J N

Site-specific genome editing in Plasmodium falciparum using engineered zinc-finger nucleases

利用工程化锌指核酸酶对恶性疟原虫进行位点特异性基因组编辑

Straimer, Judith; Lee, Marcus C S; Lee, Andrew H; Zeitler, Bryan; Williams, April E; Pearl, Jocelynn R; Zhang, Lei; Rebar, Edward J; Gregory, Philip D; Llinás, Manuel; Urnov, Fyodor D; Fidock, David A

A foundation for universal T-cell based immunotherapy: T cells engineered to express a CD19-specific chimeric-antigen-receptor and eliminate expression of endogenous TCR

基于T细胞的通用免疫疗法的基础:经基因工程改造的T细胞,使其表达CD19特异性嵌合抗原受体并消除内源性TCR的表达。

Torikai, Hiroki; Reik, Andreas; Liu, Pei-Qi; Zhou, Yuanyue; Zhang, Ling; Maiti, Sourindra; Huls, Helen; Miller, Jeffrey C; Kebriaei, Partow; Rabinovich, Brian; Lee, Dean A; Champlin, Richard E; Bonini, Chiara; Naldini, Luigi; Rebar, Edward J; Gregory, Philip D; Holmes, Michael C; Cooper, Laurence J N

In vivo genome editing restores haemostasis in a mouse model of haemophilia

体内基因组编辑可恢复血友病小鼠模型的止血功能

Li, Hojun; Haurigot, Virginia; Doyon, Yannick; Li, Tianjian; Wong, Sunnie Y; Bhagwat, Anand S; Malani, Nirav; Anguela, Xavier M; Sharma, Rajiv; Ivanciu, Lacramiora; Murphy, Samuel L; Finn, Jonathan D; Khazi, Fayaz R; Zhou, Shangzhen; Paschon, David E; Rebar, Edward J; Bushman, Frederic D; Gregory, Philip D; Holmes, Michael C; High, Katherine A

Genetic engineering of human pluripotent cells using TALE nucleases

利用TALE核酸酶对人类多能干细胞进行基因工程改造

Hockemeyer, Dirk; Wang, Haoyi; Kiani, Samira; Lai, Christine S; Gao, Qing; Cassady, John P; Cost, Gregory J; Zhang, Lei; Santiago, Yolanda; Miller, Jeffrey C; Zeitler, Bryan; Cherone, Jennifer M; Meng, Xiangdong; Hinkley, Sarah J; Rebar, Edward J; Gregory, Philip D; Urnov, Fyodor D; Jaenisch, Rudolf

Efficient targeted gene disruption in the soma and germ line of the frog Xenopus tropicalis using engineered zinc-finger nucleases.

利用工程化锌指核酸酶对非洲爪蟾的体细胞和生殖细胞进行高效的靶向基因破坏

Young John J, Cherone Jennifer M, Doyon Yannick, Ankoudinova Irina, Faraji Farhoud M, Lee Andrew H, Ngo Catherine, Guschin Dmitry Y, Paschon David E, Miller Jeffrey C, Zhang Lei, Rebar Edward J, Gregory Philip D, Urnov Fyodor D, Harland Richard M, Zeitler Bryan

Functional genomics, proteomics, and regulatory DNA analysis in isogenic settings using zinc finger nuclease-driven transgenesis into a safe harbor locus in the human genome

利用锌指核酸酶驱动的转基因技术,在人类基因组的安全港位点进行同源基因组学、蛋白质组学和调控DNA分析

DeKelver, Russell C; Choi, Vivian M; Moehle, Erica A; Paschon, David E; Hockemeyer, Dirk; Meijsing, Sebastiaan H; Sancak, Yasemin; Cui, Xiaoxia; Steine, Eveline J; Miller, Jeffrey C; Tam, Phillip; Bartsevich, Victor V; Meng, Xiangdong; Rupniewski, Igor; Gopalan, Sunita M; Sun, Helena C; Pitz, Kathleen J; Rock, Jeremy M; Zhang, Lei; Davis, Gregory D; Rebar, Edward J; Cheeseman, Iain M; Yamamoto, Keith R; Sabatini, David M; Jaenisch, Rudolf; Gregory, Philip D; Urnov, Fyodor D