Humanized mutant FUS drives progressive motor neuron degeneration without aggregation in 'FUSDelta14' knockin mice
人源化突变型FUS在“FUSDelta14”敲入小鼠中驱动进行性运动神经元退化,但不发生聚集。
期刊:Brain
影响因子:11.7
doi:10.1093/brain/awx248
Devoy, Anny; Kalmar, Bernadett; Stewart, Michelle; Park, Heesoon; Burke, Beverley; Noy, Suzanna J; Redhead, Yushi; Humphrey, Jack; Lo, Kitty; Jaeger, Julian; Mejia Maza, Alan; Sivakumar, Prasanth; Bertolin, Cinzia; Soraru, Gianni; Plagnol, Vincent; Greensmith, Linda; Acevedo Arozena, Abraham; Isaacs, Adrian M; Davies, Benjamin; Fratta, Pietro; Fisher, Elizabeth M C