Positron Emission Tomography Quantitative Assessment of Off-Target Whole-Body Biodistribution of I-124-Labeled Adeno-Associated Virus Capsids Administered to Cerebral Spinal Fluid
正电子发射断层扫描定量评估经脑脊液给药的碘-124标记腺相关病毒衣壳的非靶向全身生物分布
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2023.060
Rosenberg, Jonathan B; Fung, Edward K; Dyke, Jonathan P; De, Bishnu P; Lou, Howard; Kelly, James M; Reejhsinghani, Layla; Ricart Arbona, Rodolfo J; Sondhi, Dolan; Kaminsky, Stephen M; Cartier, Nathalie; Hinderer, Christian; Hordeaux, Juliette; Wilson, James M; Ballon, Douglas J; Crystal, Ronald G