Correction of beta-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patients
通过基因转移对儿童患者造血祖细胞中的重型β地中海贫血进行矫正
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.1002/emmm.201000083.
Emanuela Anna Roselli,Riccardo Mezzadra, Marta Claudia Frittoli, Giulietta Maruggi, Erika Biral, Fulvio Mavilio, Fabrizio Mastropietro, Antonio Amato, Giovanni Tonon, Chiara Refaldi, Maria Domenica Cappellini, Marco Andreani, Guido Lucarelli, Maria Grazia Roncarolo, Sarah Marktel, Giuliana Ferrari