Implications of circulating neurofilaments for spinal muscular atrophy treatment early in life: A case series
循环神经丝对早期脊髓性肌萎缩症治疗的意义:一系列病例
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2021.10.011
Christiano R R Alves, Marco Petrillo, Rebecca Spellman, Reid Garner, Ren Zhang, Michael Kiefer, Sarah Simeone, Jihee Sohn, Eric J Eichelberger, Emma Rodrigues, Elizabeth A Arruda, Elise L Townsend, Wildon Farwell, Kathryn J Swoboda