日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Implications of circulating neurofilaments for spinal muscular atrophy treatment early in life: A case series

循环神经丝对早期脊髓性肌萎缩症治疗的意义:一系列病例

Christiano R R Alves, Marco Petrillo, Rebecca Spellman, Reid Garner, Ren Zhang, Michael Kiefer, Sarah Simeone, Jihee Sohn, Eric J Eichelberger, Emma Rodrigues, Elizabeth A Arruda, Elise L Townsend, Wildon Farwell, Kathryn J Swoboda

Whole-blood dysregulation of actin-cytoskeleton pathway in adult spinal muscular atrophy patients

成年脊髓性肌萎缩症患者全血肌动蛋白细胞骨架通路失调

Jennifer J Siranosian, Flavia C Nery, Christiano R R Alves, Benjamin A Siranosian, Nicholas J Lyons, Eric J Eichelberger, Reid Garner, Salomé Da Silva Duarte Lepez, Alec J Johnstone, Aravind Subramanian, Kathryn J Swoboda