日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cerebral organoids containing an AUTS2 missense variant model microcephaly

含有 AUTS2 错义变异模型的脑类器官可导致小头畸形

Summer R Fair, Wesley Schwind, Dominic L Julian, Alecia Biel, Gongbo Guo, Ryan Rutherford, Swetha Ramadesikan, Jesse Westfall, Katherine E Miller, Meisam Naeimi Kararoudi, Scott E Hickey, Theresa Mihalic Mosher, Kim L McBride, Reid Neinast, James Fitch, Dean A Lee, Peter White, Richard K Wilson, Tra

Promising AAV.U7snRNAs vectors targeting DMPK improve DM1 hallmarks in patient-derived cell lines

靶向DMPK的AAV.U7snRNA载体有望改善患者来源细胞系中的DM1特征。

Camila F Almeida ,Florence Robriquet ,Tatyana A Vetter ,Nianyuan Huang ,Reid Neinast ,Lumariz Hernandez-Rosario ,Dhanarajan Rajakumar ,W David Arnold ,Kim L McBride ,Kevin M Flanigan ,Robert B Weiss ,Nicolas Wein

miR-155 targets histone deacetylase 4 (HDAC4) and impairs transcriptional activity of B-cell lymphoma 6 (BCL6) in the Eμ-miR-155 transgenic mouse model

miR-155 靶向组蛋白去乙酰化酶 4 (HDAC4) 并削弱 Eμ-miR-155 转基因小鼠模型中 B 细胞淋巴瘤 6 (BCL6) 的转录活性

Sukhinder K Sandhu, Stefano Volinia, Stefan Costinean, Marco Galasso, Reid Neinast, Ramasamy Santhanam, Mark R Parthun, Danilo Perrotti, Guido Marcucci, Ramiro Garzon, Carlo M Croce