In vivo topical gene therapy for recessive dystrophic epidermolysis bullosa: a phase 1 and 2 trial
隐性营养不良型大疱性表皮松解症的体内局部基因治疗:1 期和 2 期试验
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-022-01737-y
Irina Gurevich, Pooja Agarwal, PeiPei Zhang, John A Dolorito, Stacie Oliver, Henry Liu, Nicholas Reitze, Nikhil Sarma, Isin Sinem Bagci, Kunju Sridhar, Visesha Kakarla, Vamsi K Yenamandra, Mark O'Malley, Marco Prisco, Sara F Tufa, Douglas R Keene, Andrew P South, Suma M Krishnan, M Peter Marinkovich