A Quantitative In Vitro Potency Assay for Adeno-Associated Virus Vectors Encoding for the UGT1A1 Transgene
编码 UGT1A1 转基因的腺相关病毒载体的体外定量效力测定
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2020.06.002
Sem J Aronson, Robert S Bakker, Sascha Moenis, Remco van Dijk, Giulia Bortolussi, Fanny Collaud, Xiaoxia Shi, Suzanne Duijst, Lysbeth Ten Bloemendaal, Giuseppe Ronzitti, Andrés F Muro, Federico Mingozzi, Ulrich Beuers, Piter J Bosma