Late-onset Pompe disease (LOPD) in Belgium: clinical characteristics and outcome measures
比利时晚发型庞贝病(LOPD):临床特征和预后指标
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-020-01353-4
Vanherpe, P; Fieuws, S; D'Hondt, A; Bleyenheuft, C; Demaerel, P; De Bleecker, J; Van den Bergh, P; Baets, J; Remiche, G; Verhoeven, K; Delstanche, S; Toussaint, M; Buyse, B; Van Damme, P; Depuydt, C E; Claeys, K G