日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Q1291H-CFTR molecular dynamics simulations and ex vivo theratyping in nasal epithelial models and clinical response to elexacaftor/tezacaftor/ivacaftor in a Q1291H/F508del patient

Q1291H-CFTR 分子动力学模拟和鼻上皮模型中的体外治疗分型以及 Q1291H/F508del 患者对 elexacaftor/tezacaftor/ivacaftor 的临床反应

Katelin M Allan, Miro A Astore, Egi Kardia, Sharon L Wong, Laura K Fawcett, Jessica L Bell, Simone Visser, Po-Chia Chen, Renate Griffith, Adam Jaffe, Sheila Sivam, Orazio Vittorio, Serdar Kuyucak, Shafagh A Waters

Molecular Dynamics and Theratyping in Airway and Gut Organoids Reveal R352Q-CFTR Conductance Defect

气道和肠道类器官中的分子动力学和治疗分型揭示了 R352Q-CFTR 传导缺陷

Sharon L Wong, Nikhil T Awatade, Miro A Astore, Katelin M Allan, Michael J Carnell, Iveta Slapetova, Po-Chia Chen, Jeffry Setiadi, Elvis Pandzic, Laura K Fawcett, John R Widger, Renee M Whan, Renate Griffith, Chee Y Ooi, Serdar Kuyucak, Adam Jaffe, Shafagh A Waters

S945L-CFTR molecular dynamics, functional characterization and tezacaftor/ivacaftor efficacy in vivo and in vitro in matched pediatric patient-derived cell models

S945L-CFTR 分子动力学、功能表征和 tezacaftor/ivacaftor 在匹配的儿科患者来源细胞模型中的体内和体外疗效

Katelin M Allan, Miro A Astore, Laura K Fawcett, Sharon L Wong, Po-Chia Chen, Renate Griffith, Adam Jaffe, Serdar Kuyucak, Shafagh A Waters

Molecular dynamics and functional characterization of I37R-CFTR lasso mutation provide insights into channel gating activity

I37R-CFTR 套索突变的分子动力学和功能表征为通道门控活性提供了见解

Sharon L Wong, Nikhil T Awatade, Miro A Astore, Katelin M Allan, Michael J Carnell, Iveta Slapetova, Po-Chia Chen, Alexander Capraro, Laura K Fawcett, Renee M Whan, Renate Griffith, Chee Y Ooi, Serdar Kuyucak, Adam Jaffe, Shafagh A Waters