日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Phase 1 pilot study for hemophilia-A: AAV8 vector with prophylactic tacrolimus-glucocorticoid achieves therapeutic FVIII activity

针对A型血友病的I期试点研究:AAV8载体联合预防性他克莫司-糖皮质激素治疗可达到治疗性FVIII活性。

Liu, Wei; Pei, Xiaolei; Yu, Tenghui; Xu, Bingqi; Dai, Xinyue; Xue, Feng; Chen, Lingling; Wang, Xiaolin; Wang, Yuhua; Chen, Yunfei; Liu, Xiaofan; Fu, Rongfeng; Wang, Wentian; Chi, Ying; Li, Hui Yuan; Yang, Renchi; Zhang, Lei

Factor IX-Padua AAV gene therapy in hemophilia B: phases 1/2 and 3 trials

IX因子-Padua AAV基因疗法治疗B型血友病:1/2期和3期试验

Xue, Feng; Ju, Mankai; Zhu, Tienan; Zhou, Zeping; Sun, Jing; Yang, Linhua; Yan, Zhenyu; Zhou, Hu; Du, Xin; Zheng, ChangCheng; Zheng, Jing; Wu, Xia; Du, Zengmin; Jiang, Wei; Yang, Caifeng; Xiao, Xiao; Liu, Wei; Yang, Renchi; Zhang, Lei

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial

marstacimab预防治疗A/B型血友病伴抑制剂的疗效和安全性:来自3期BASIS试验的结果

Matino, Davide; Acharya, Suchitra S; Taylor, Carrie Turich; Sun, Pengling; Agathon, Delphine; Raje, Sangeeta; Gould, Travis; Palladino, Andrew; Mahlangu, Johnny; Lissitchkov, Toshko; Todorova, Mariya; Chan, Anthony; Carcao, Manuel; Sun, Jing; Yang, Renchi; Wu, Runhui; Jin, Chenghao; Zeng, Xiaojing; Boban, Ana; Bilic, Ernest; Frenzel, Laurent; Fung Chan, Godfrey Chi; Kong Li, Chi; Apte, Shashikant; Choraria, Nirmalkumar; Chistolini, Antonio; Marchesini, Emanuela; Peyvandi, Flora; Fujii, Teruhisa; Matsushita, Tadashi; Kaneda, Makoto; Lyu, Chuhl Joo; Park, Young Shil; Kim, SungEun; Martinez, Laura Villarreal; Adrian, Javier Morales; Wali, Yasser; Al Khabori, Murtadha; Kurtov, Igor; Alzahrani, Hazzaa; Zaher, Galila; Micic, Dragan; Miljic, Predrag; Kostic, Gordana; Vucic, Miodrag; Djurdjevic, Predrag; Hidalgo, Olga Benitez; Porras, Jose Gonzalez; Jiménez-Yuste, Víctor; Calvo Villas, Jose Manuel; Lopez Fernandez, Maria Fernanda; Albayrak, Canan; Okan, Vahap; Balkan, Can; Sahin, Fahri; Antmen, Ali; Unal, Ekrem; Visweshwar, Nathan; Sharathkumar, Anjali; Kruse-Jarres, Rebecca

Daratumumab in patients with immune thrombocytopenia: a single-center, open-label, phase 2 trial

Daratumumab治疗免疫性血小板减少症患者:一项单中心、开放标签的II期试验

Chen, Yunfei; Hua, Zhengjie; Xu, Yanmei; Chen, Jia; Wen, Qing; Sun, Ting; Li, Huiyuan; Liu, Xiaofan; Fu, Rongfeng; Ju, Mankai; Xue, Feng; Liu, Wei; Dong, Huan; Gu, Wenjing; Dai, Xinyue; Wang, Wentian; Chi, Ying; Pei, Xiaolei; Yang, Renchi; Zhang, Lei

Recombinant von Willebrand factor for von Willebrand disease: mechanism of action and clinical application

重组血管性血友病因子治疗血管性血友病:作用机制及临床应用

Hua, Zhengjie; Miao, Wenjuan; Zhang, Ping; Yang, Renchi

MPIG6B-related thrombocytopenia and myelofibrosis: A case report

MPIG6B相关血小板减少症和骨髓纤维化:病例报告

Wang, Xin; Xue, Feng; Zhang, Lei; Yang, Renchi

Anti-CD38 monoclonal antibody CM313 for primary immune thrombocytopenia: multicentre, randomised, placebo controlled, phase 2 trial

抗CD38单克隆抗体CM313治疗原发性免疫性血小板减少症:一项多中心、随机、安慰剂对照的II期临床试验

Chen, Yunfei; Xu, Yanmei; Dai, Jiawen; Sun, Ting; Li, Huiyuan; Hua, Zhengjie; Zhou, Zeping; Zhou, Hu; Yan, Zhenyu; Zhao, Xingli; Xue, Feng; Liu, Wei; Liu, Xiaofan; Fu, Rongfeng; Wang, Wentian; Chi, Ying; Dong, Huan; Ju, Mankai; Dai, Xinyue; Gu, Wenjing; Pei, Xiaolei; Yang, Renchi; Zhang, Lei

Marstacimab prophylaxis in hemophilia A/B without inhibitors: results from the phase 3 BASIS trial

在无抑制剂的A/B型血友病患者中应用马斯替单抗进行预防性治疗:来自3期BASIS试验的结果

Matino, Davide; Palladino, Andrew; Taylor, Carrie Turich; Hwang, Eunhee; Raje, Sangeeta; Nayak, Satyaprakash; McDonald, Regina; Acharya, Suchitra S; Mahlangu, Johnny; Jiménez-Yuste, Victor; Choraria, Nirmalkumar; Yang, Renchi; Li, Chi-Kong; Al-Khabori, Murtadha; Wali, Yasser; Morales Adrián, Javier; Park, Young-Shil; Zülfikar, O Bülent; Teeter, John

First-in-human pharmacokinetic, safety, and preliminary efficacy studies of single- and multiple-dose FRSW117, a novel PEGylated recombinant factor VIII-Fc fusion protein with an extended half-life, in patients with severe hemophilia A

首次在重型血友病A患者中开展了单剂量和多剂量FRSW117(一种新型聚乙二醇化重组因子VIII-Fc融合蛋白,具有延长的半衰期)的人体药代动力学、安全性和初步疗效研究。

Xue, Feng; Guo, Shuxia; Liu, Ping; Chen, Weizhi; Chen, Yun; Wen, Qing; Hua, Haiying; Cao, Yu; Feng, Xianqi; Sun, Jing; Xu, Chongyuan; Yang, Renchi

Efficacy and safety of vascular-targeting agents in advanced soft tissue sarcoma: a systematic review and network meta-analysis

血管靶向药物治疗晚期软组织肉瘤的疗效和安全性:系统评价和网络荟萃分析

Wang, Yan; Xu, Hangcheng; Sa, Qiang; Zhou, Yiran; Cheng, Hong; Gao, Renchi; Xu, Binghe; Wang, Jiayu