A new glucocerebrosidase-deficient neuronal cell model provides a tool to probe pathophysiology and therapeutics for Gaucher disease
新的缺乏葡萄糖脑苷脂酶的神经元细胞模型为探索戈谢病的病理生理学和治疗方法提供了工具
期刊:Disease Models & Mechanisms
影响因子:4
doi:10.1242/dmm.024588
Wendy Westbroek, Matthew Nguyen, Marina Siebert, Taylor Lindstrom, Robert A Burnett, Elma Aflaki, Olive Jung, Rafael Tamargo, Jorge L Rodriguez-Gil, Walter Acosta, An Hendrix, Bahafta Behre, Nahid Tayebi, Hideji Fujiwara, Rohini Sidhu, Benoit Renvoise, Edward I Ginns, Amalia Dutra, Evgenia Pak, Caro