CRISPR/Cas-mediated activation of genes associated with inherited retinal dystrophies in human cells for diagnostic purposes
利用 CRISPR/Cas 介导的基因编辑技术激活人类细胞中与遗传性视网膜营养不良相关的基因，以用于诊断目的
期刊:JCI Insight
影响因子:6.1
doi:10.1172/jci.insight.189615
Weber, Valentin J; Reschigna, Alice; Gerhardt, Maximilian J; Heigl, Thomas; Hinrichsmeyer, Klara S; den Engel, Sander van; Otify, Dina Y; Gavrilov, Zoran; Blaser, Frank; Meneau, Isabelle; Betz, Christian; Bolz, Hanno J; Biel, Martin; Michalakis, Stylianos; Becirovic, Elvir
