日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Therapeutic development for Canavan disease using patient iPSCs introduced with the wild-type ASPA gene

利用导入野生型ASPA基因的患者iPSCs进行卡纳万病治疗开发

Jianfei Chao ,Lizhao Feng ,Peng Ye ,Xianwei Chen ,Qi Cui ,Guihua Sun ,Tao Zhou ,E Tian ,Wendong Li ,Weidong Hu ,Arthur D Riggs ,Reuben Matalon ,Yanhong Shi

Cell-Based Therapy for Canavan Disease Using Human iPSC-Derived NPCs and OPCs

使用人类 iPSC 衍生的 NPC 和 OPC 进行 Canavan 病的细胞疗法

Lizhao Feng, Jianfei Chao, E Tian, Li Li, Peng Ye, Mi Zhang, Xianwei Chen, Qi Cui, Guihua Sun, Tao Zhou, Gerardo Felix, Yue Qin, Wendong Li, Edward David Meza, Jeremy Klein, Lucy Ghoda, Weidong Hu, Yonglun Luo, Wei Dang, David Hsu, Joseph Gold, Steven A Goldman, Reuben Matalon, Yanhong Shi

Redirecting N-acetylaspartate metabolism in the central nervous system normalizes myelination and rescues Canavan disease

改变中枢神经系统中的 N-乙酰天冬氨酸代谢可使髓鞘形成正常化并挽救卡纳万病

Dominic J Gessler, Danning Li, Hongxia Xu, Qin Su, Julio Sanmiguel, Serafettin Tuncer, Constance Moore, Jean King, Reuben Matalon, Guangping Gao