日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preformed Vesicle Approach to LNP Manufacturing Enhances Retinal mRNA Delivery.

预成型囊泡法制备LNP可增强视网膜mRNA递送

Eygeris Yulia, Henderson Michael I, Curtis Allison G, Jozić Antony, Stoddard Jonathan, Reynaga Rene, Chirco Kathleen R, Su Grace Li-Na, Neuringer Martha, Lauer Andreas K, Ryals Renee C, Sahay Gaurav

Thiophene-based lipids for mRNA delivery to pulmonary and retinal tissues

基于噻吩的脂质体用于将mRNA递送至肺部和视网膜组织

Eygeris, Yulia; Gupta, Mohit; Kim, Jeonghwan; Jozic, Antony; Gautam, Milan; Renner, Jonas; Nelson, Dylan; Bloom, Elissa; Tuttle, Adam; Stoddard, Jonathan; Reynaga, Rene; Neuringer, Martha; Lauer, Andreas K; Ryals, Renee C; Sahay, Gaurav

Development of a translatable gene augmentation therapy for CNGB1-retinitis pigmentosa

开发一种可转化的基因增强疗法用于治疗 CNGB1 基因突变引起的视网膜色素变性

Occelli, Laurence M; Zobel, Lena; Stoddard, Jonathan; Wagner, Johanna; Pasmanter, Nathaniel; Querubin, Janice; Renner, Lauren M; Reynaga, Rene; Winkler, Paige A; Sun, Kelian; Marinho, Luis Felipe L P; O'Riordan, Catherine R; Frederick, Amy; Lauer, Andreas; Tsang, Stephen H; Hauswirth, William W; McGill, Trevor J; Neuringer, Martha; Michalakis, Stylianos; Petersen-Jones, Simon M