Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing
通过结构导向的化学修饰修饰引导RNA,可以实现高效的非病毒体内基因组编辑。
期刊:Nature Biotechnology
影响因子:41.7
doi:10.1038/nbt.4005
Yin, Hao; Song, Chun-Qing; Suresh, Sneha; Wu, Qiongqiong; Walsh, Stephen; Rhym, Luke Hyunsik; Mintzer, Esther; Bolukbasi, Mehmet Fatih; Zhu, Lihua Julie; Kauffman, Kevin; Mou, Haiwei; Oberholzer, Alicia; Ding, Junmei; Kwan, Suet-Yan; Bogorad, Roman L; Zatsepin, Timofei; Koteliansky, Victor; Wolfe, Scot A; Xue, Wen; Langer, Robert; Anderson, Daniel G