日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A novel gene therapy platform for the treatment of type 2 diabetes and obesity.

一种用于治疗2型糖尿病和肥胖症的新型基因治疗平台。

Lourie Jared, Goraltchouk Alex, Hollander Judith M, Berger Nicolas J, Rosen H Grace, Fujishiro Atsutaro A, Luppino Francesco, Seregin Alexey, Rhym Luke, Zou Kai

Adenine base editing in an adult mouse model of tyrosinaemia

酪氨酸血症成年小鼠模型中的腺嘌呤碱基编辑

Song, Chun-Qing; Jiang, Tingting; Richter, Michelle; Rhym, Luke H; Koblan, Luke W; Zafra, Maria Paz; Schatoff, Emma M; Doman, Jordan L; Cao, Yueying; Dow, Lukas E; Zhu, Lihua Julie; Anderson, Daniel G; Liu, David R; Yin, Hao; Xue, Wen

Chemical modifications of adenine base editor mRNA and guide RNA expand its application scope

腺嘌呤碱基编辑器mRNA和引导RNA的化学修饰拓展了其应用范围

Tingting Jiang, Jordana M Henderson, Kevin Coote, Yi Cheng, Hillary C Valley, Xiao-Ou Zhang, Qin Wang, Luke H Rhym, Yueying Cao, Gregory A Newby, Hermann Bihler, Martin Mense, Zhiping Weng, Daniel G Anderson, Anton P McCaffrey, David R Liu, Wen Xue

Downregulation of the Arg/N-degron Pathway Sensitizes Cancer Cells to Chemotherapy In Vivo

Arg/N-降解途径下调使癌细胞对体内化疗敏感

Dominique Leboeuf, Tatiana Abakumova, Tatiana Prikazchikova, Luke Rhym, Daniel G Anderson, Timofei S Zatsepin, Konstantin I Piatkov

Customizable Lipid Nanoparticle Materials for the Delivery of siRNAs and mRNAs

用于递送siRNA和mRNA的可定制脂质纳米颗粒材料

Fenton, Owen S; Kauffman, Kevin J; McClellan, Rebecca L; Kaczmarek, James C; Zeng, Manhao D; Andresen, Jason L; Rhym, Luke H; Heartlein, Michael W; DeRosa, Frank; Anderson, Daniel G

Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing

通过结构导向的化学修饰修饰引导RNA,可以实现高效的非病毒体内基因组编辑。

Yin, Hao; Song, Chun-Qing; Suresh, Sneha; Wu, Qiongqiong; Walsh, Stephen; Rhym, Luke Hyunsik; Mintzer, Esther; Bolukbasi, Mehmet Fatih; Zhu, Lihua Julie; Kauffman, Kevin; Mou, Haiwei; Oberholzer, Alicia; Ding, Junmei; Kwan, Suet-Yan; Bogorad, Roman L; Zatsepin, Timofei; Koteliansky, Victor; Wolfe, Scot A; Xue, Wen; Langer, Robert; Anderson, Daniel G