日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Selective AMPKβ1 activation induces fetal hemoglobin in human erythroid cells and sickle cell mice via the noncanonical NRF2 pathway

选择性激活AMPKβ1可通过非经典NRF2通路诱导人红细胞和镰状细胞小鼠产生胎儿血红蛋白。

Yannis Hara ,Viktor T Lemgart ,Samuel Lessard ,Courtney J Mercadante ,Jean-Antoine Ribeil ,Alexandra Hicks ,Pauline Rimmele ,David R Light

XTX301, a Tumor-Activated Interleukin-12 Has the Potential to Widen the Therapeutic Index of IL12 Treatment for Solid Tumors as Evidenced by Preclinical Studies

XTX301 是一种肿瘤激活的白细胞介素-12,临床前研究表明其具有拓宽 IL-12 治疗实体瘤的治疗指数的潜力。

Ekta Patel ,Natalia V Malkova ,David Crowe ,Magali Pederzoli-Ribeil ,Damiano Fantini ,Manoussa Fanny ,Hanumantha Rao Madala ,Kurt A Jenkins ,Oleg Yerov ,Justin Greene ,Wilson Guzman ,Caitlin O'Toole ,Jacob Taylor ,Rebekah K O'Donnell ,Parker Johnson ,Bernard B Lanter ,Brian Ames ,Jia Chen ,Sallyann Vu ,Hsin-Jung Wu ,Susan Cantin ,Megan McLaughlin ,Yu-Shan S Hsiao ,Dheeraj S Tomar ,Raphael Rozenfeld ,Lakshmanan Thiruneelakantapillai ,Ronan C O'Hagan ,Benjamin Nicholson ,Jennifer O'Neil ,Carl Uli Bialucha

XTX101, a tumor-activated, Fc-enhanced anti-CTLA-4 monoclonal antibody, demonstrates tumor-growth inhibition and tumor-selective pharmacodynamics in mouse models of cancer

XTX101是一种肿瘤激活的、Fc增强的抗CTLA-4单克隆抗体,在小鼠癌症模型中表现出肿瘤生长抑制作用和肿瘤选择性药效学。

Kurt A Jenkins ,Miso Park ,Magali Pederzoli-Ribeil ,Ugur Eskiocak ,Parker Johnson ,Wilson Guzman ,Megan McLaughlin ,Deborah Moore-Lai ,Caitlin O'Toole ,Zhen Liu ,Benjamin Nicholson ,Veronica Flesch ,Huawei Qiu ,Tim Clackson ,Ronan C O'Hagan ,Ulrich Rodeck ,Margaret Karow ,Jennifer O'Neil ,John C Williams

Lovo-cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB-206 study

Lovo-cel基因疗法治疗镰状细胞病:HGB-206研究初期组的治疗过程演变和结果

Kanter, Julie; Thompson, Alexis A; Pierciey, Francis J Jr; Hsieh, Matthew; Uchida, Naoya; Leboulch, Philippe; Schmidt, Manfred; Bonner, Melissa; Guo, Ruiting; Miller, Alex; Ribeil, Jean-Antoine; Davidson, David; Asmal, Mohammed; Walters, Mark C; Tisdale, John F

SGK1 inhibition induces fetal hemoglobin expression and delays polymerization in sickle erythroid cells

SGK1抑制可诱导胎儿血红蛋白表达并延缓镰状红细胞的聚合。

Hara, Yannis; Lemgart, Viktor T; Halland, Nis; Mahdaviani, Kiana; Ribeil, Jean-Antoine; Lessard, Samuel; Hicks, Alexandra; Light, David R

Sickle Cell Trait Modulates the Proteome and Phosphoproteome of Plasmodium falciparum-Infected Erythrocytes

镰状细胞性状调节恶性疟原虫感染红细胞的蛋白质组和磷酸化蛋白质组

Margaux Chauvet, Cerina Chhuon, Joanna Lipecka, Sébastien Dechavanne, Célia Dechavanne, Murielle Lohezic, Margherita Ortalli, Damien Pineau, Jean-Antoine Ribeil, Sandra Manceau, Caroline Le Van Kim, Adrian J F Luty, Florence Migot-Nabias, Slim Azouzi, Ida Chiara Guerrera, Anaïs Merckx

A novel, highly potent and selective phosphodiesterase-9 inhibitor for the treatment of sickle cell disease

一种新型、高效且选择性强的磷酸二酯酶-9抑制剂,用于治疗镰状细胞病

McArthur, James G; Svenstrup, Niels; Chen, Chunsheng; Fricot, Aurelie; Carvalho, Caroline; Nguyen, Julia; Nguyen, Phong; Parachikova, Anna; Abdulla, Fuad; Vercellotti, Gregory M; Hermine, Olivier; Edwards, Dave; Ribeil, Jean-Antoine; Belcher, John D; Maciel, Thiago T

Primary Hyperparathyroidism in Sickle Cell Disease: An Unknown Complication of the Disease in Adulthood

镰状细胞病原发性甲状旁腺功能亢进症:成人期一种未知的并发症

Denoix, Elsa; Bomahou, Charlène; Clavier, Lorraine; Ribeil, Jean-Antoine; Lionnet, François; Bartolucci, Pablo; Courbebaisse, Marie; Pouchot, Jacques; Arlet, Jean-Benoît

Sotatercept, a novel transforming growth factor β ligand trap, improves anemia in β-thalassemia: a phase II, open-label, dose-finding study

索他西普(Sotatercept)是一种新型转化生长因子β配体捕获剂,可改善β-地中海贫血患者的贫血症状:一项II期开放标签剂量探索研究

Cappellini, Maria Domenica; Porter, John; Origa, Raffaella; Forni, Gian Luca; Voskaridou, Ersi; Galactéros, Frédéric; Taher, Ali T; Arlet, Jean-Benoît; Ribeil, Jean-Antoine; Garbowski, Maciej; Graziadei, Giovanna; Brouzes, Chantal; Semeraro, Michaela; Laadem, Abderrahmane; Miteva, Dimana; Zou, Jun; Sung, Victoria; Zinger, Tatiana; Attie, Kenneth M; Hermine, Olivier

Transfusion-related adverse events are decreased in pregnant women with sickle cell disease by a change in policy from systematic transfusion to prophylactic oxygen therapy at home: A retrospective survey by the international sickle cell disease observatory

国际镰状细胞病观察站的一项回顾性调查显示,通过改变治疗策略,从系统性输血改为居家预防性氧疗,可以减少镰状细胞病孕妇的输血相关不良事件。

Ribeil, Jean-Antoine; Labopin, Myriam; Stanislas, Aurélie; Deloison, Benjamin; Lemercier, Delphine; Habibi, Anoosha; Albinni, Souha; Charlier, Caroline; Lortholary, Olivier; Lefrere, François; De Montalembert, Mariane; Blanche, Stéphane; Galactéros, Frédéric; Tréluyer, Jean-Marc; Gluckman, Eliane; Ville, Yves; Joseph, Laure; Delville, Marianne; Benachi, Alexandra; Cavazzana, Marina