日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy (OTL-203) for Hurler syndrome

造血干细胞和祖细胞基因治疗(OTL-203)治疗赫勒综合征的非神经系统、非骨骼结局

Tucci, Francesca; Uria Oficialdegui, M Luz; Consiglieri, Giulia; Cossutta, Matilde; Filisetti, Chiara; Fumagalli, Francesca; Butera, Carla; Santangelo, Roberto; Colombo, Michele; Manitto, Maria Pia; Stoppani, Monica; Martina, Elisabetta; Danè, Giulia; Camesasca, Chiara; Risca, Giulia; De Pellegrin, Maurizio; Scarparo, Stefano; Sarzana, Marina; Puricelli, Cristina; Galimberti, Stefania; Darin, Silvia; Silvani, Paolo; Bonanomi, Sonia; Gasperini, Serena; Naldini, Luigi; Gentner, Bernhard; Parini, Rossella; Del Toro, Mireia; Diaz-de-Heredia, Cristina; Aiuti, Alessandro; Bernardo, Maria Ester

Targeting oncogene-induced senescence in ETV6::RUNX1 pre-leukemic cells.

靶向 ETV6::RUNX1 白血病前期细胞中癌基因诱导的衰老。

Acunzo Denise, Bertagna Mayla, Risca Giulia, Beneforti Linda, Bresolin Silvia, Galimberti Stefania, Sánchez-García Isidro, Biondi Andrea, Cazzaniga Giovanni, Palmi Chiara

The Impact of Comorbidities on Health-Related Quality of Life Among Patients with Rheumatoid Arthritis

合并症对类风湿性关节炎患者健康相关生活质量的影响

Vlad, Adriana Liliana; Popazu, Corina Risca; Lescai, Alina-Maria; Prisacaru, Daniela-Ioanina; Voinescu, Doina Carina; Baltă, Alexia Anastasia Stefania

A nucleosome switch primes hepatitis B virus infection

核小体转换启动乙型肝炎病毒感染

Nicholas A Prescott ,Tracy Biaco ,Andrés Mansisidor ,Yaron Bram ,Justin Rendleman ,Sarah C Faulkner ,Abigail A Lemmon ,Christine Lim ,Rachel Tiersky ,Eralda Salataj ,Liliana Garcia-Martinez ,Rodrigo L Borges ,Lluis Morey ,Pierre-Jacques Hamard ,Richard P Koche ,Viviana I Risca ,Robert E Schwartz ,Yael David

Donor-derived CARCIK-CD19 cells engineered with Sleeping Beauty transposon in acute lymphoblastic leukemia relapsed after allogeneic transplantation

经Sleeping Beauty转座子改造的供体来源CARCIK-CD19细胞在同种异体移植后急性淋巴细胞白血病复发

Lussana, Federico; Magnani, Chiara F; Galimberti, Stefania; Gritti, Giuseppe; Gaipa, Giuseppe; Belotti, Daniela; Cabiati, Benedetta; Napolitano, Sara; Ferrari, Silvia; Moretti, Alex; Buracchi, Chiara; Borleri, Gian Maria; Rambaldi, Benedetta; Rizzuto, Giuliana; Grassi, Anna; Paganessi, Muriel; Meli, Cristian; Tettamanti, Sarah; Risca, Giulia; Pais, Giulia; Spinozzi, Giulio; Benedicenti, Fabrizio; Cazzaniga, Giovanni; Capelli, Chiara; Gotti, Elisa; Introna, Martino; Golay, Josée; Montini, Eugenio; Balduzzi, Adriana; Valsecchi, Maria Grazia; Dastoli, Giuseppe; Rambaldi, Alessandro; Biondi, Andrea

Acquisition of an immunosuppressive microenvironment after anti-CD19 CAR T-cell therapy is associated with T-cell dysfunction and resistance

抗CD19 CAR-T细胞疗法后免疫抑制性微环境的形成与T细胞功能障碍和耐药性相关。

Ponzo, Marianna; Drufuca, Lorenzo; Buracchi, Chiara; Sindoni, Marco M; Nucera, Silvia; Bugarin, Cristina; Bason, Ramona; Rossetti, Grazisa; Bonnal, Raoul; Meli, Cristian; Rambaldi, Benedetta; Lussana, Federico; Ferrari, Silvia; Moretti, Alex; Dastoli, Giuseppe; Risca, Giulia; Pellegrino, Christian; Manz, Markus G; Galimberti, Stefania; Rambaldi, Alessandro; Gaipa, Giuseppe; Biondi, Andrea; Pagani, Massimiliano; Magnani, Chiara F

Mid-term comparison of new-onset AHRE between His bundle and left bundle branch area pacing in patients with AV block

中期比较希氏束起搏和左束支区域起搏在房室传导阻滞患者中新发房性高活动性心律失常(AHRE)的发生率。

Pestrea, Catalin; Cicala, Ecaterina; Enache, Roxana; Rusu, Marcela; Gavrilescu, Radu; Vaduva, Adrian; Risca, Sever; Clapon, Dana; Ortan, Florin

ChromBPNet: bias factorized, base-resolution deep learning models of chromatin accessibility reveal cis-regulatory sequence syntax, transcription factor footprints and regulatory variants

ChromBPNet:基于偏差分解的、碱基分辨率的染色质可及性深度学习模型揭示顺式调控序列语法、转录因子足迹和调控变异

Pampari, Anusri; Shcherbina, Anna; Kvon, Evgeny Z; Kosicki, Michael; Nair, Surag; Kundu, Soumya; Kathiria, Arwa S; Risca, Viviana I; Kuningas, Kristiina; Alasoo, Kaur; Greenleaf, William James; Pennacchio, Len A; Kundaje, Anshul

Direct measurement of sub-kilobase chromatin structure reveals that linker histone H1 broadly compacts chromatin, with differential impact amongst epigenetic states

对亚千碱基染色质结构的直接测量表明,连接组蛋白H1广泛地压缩染色质,且对不同表观遗传状态的影响存在差异。

Canaj, Hera; Duba, Irene; Mansisidor, Andres; Scortea, Andrew; Johnson, Ryan; Pinto, Hugo; Ou, Arnold; Pagane, Nicole; Pae, Juhee; Fyodorov, Dmitry; Skoultchi, Arthur I; Risca, Viviana I

Multicentric Longitudinal Prospective Study in a European Cohort of MYO7A Patients: Disease Course and Implications for Gene Therapy

一项针对欧洲MYO7A患者队列的多中心纵向前瞻性研究:疾病进程及其对基因治疗的意义

Testa, Francesco; Carreño, Ester; van den Born, L Ingeborgh; Melillo, Paolo; Perea-Romero, Irene; Di Iorio, Valentina; Risca, Giulia; Iodice, Clemente Maria; Pennings, Ronald J E; Karali, Marianthi; Banfi, Sandro; Auricchio, Alberto; Galimberti, Stefania; Ayuso, Carmen; Simonelli, Francesca