日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Hematopoietic stem cell transplantation is effective in achieving long-term survival for post-aplastic anemia myeloid neoplasms: the EBMT Severe Aplastic Anemia Report

造血干细胞移植可有效提高再生障碍性贫血后髓系肿瘤患者的长期生存率:EBMT重型再生障碍性贫血报告

Prata, Pedro Henrique; Eikema, Dirk-Jan; Piepenbroek, Brian; Kulasekararaj, Austin; Drexler, Beatrice; Tjon, Jennifer M-L; Vaht, Krista; Aljurf, Mahmoud; Chevallier, Patrice; Gedde-Dahl, Tobias; Kaare, Ain; Salmenniemi, Urpu; Schroeder, Thomas; Byrne, Jenny; Cornillon, Jérôme; Barraco, Fiorenza; Maertens, Johan; Tholouli, Eleni; Platzbecker, Uwe; Kröger, Nicolaus; Blaise, Didier; Sica, Simona; Zeiser, Robert; Risitano, Antonio Maria; De Latour, Régis Peffault; Anemia Working Party, Ebmt Severe Aplastic

Efficacy and safety of vemircopan as monotherapy in patients with paroxysmal nocturnal hemoglobinuria

维米尔可泮单药治疗阵发性睡眠性血红蛋白尿症患者的疗效和安全性

Kulasekararaj, Austin; Browett, Peter; Risitano, Antonio M; Patriquin, Christopher J; Yenerel, Mustafa N; Marceau, Daniele; Sahin, Fahri; Algarra, J Lorenzo; Ogawa, Masayo; Yu, Ji; Cross, Nicholas Bruce; Notaro, Rosario; Lee, Jong Wook; Brodsky, Robert A

Allogeneic hematopoietic stem cell transplantation in ERCC6L2 disease

ERCC6L2疾病的异基因造血干细胞移植

Hakkarainen, Marja; Sicre de Fontbrune, Flore; Kaaja, Ilse; Douglas, Suvi; Dalle, Jean-Hugues; Risitano, Antonio Maria; Kulasekararaj, Austin; Alsultan, Abdulrahman; Cutler, Corey; Ho, Vincent T; Hellström-Lindberg, Eva; Mielke, Stephan; Myhre, Anders E; Rihani, Rawad; Shanap, Mayada Abu; Hashem, Hasan; Shimamura, Akiko; Rowe, R Grant; Auer, Franziska; Beier, Fabian; Desnica, Lana; Hough, Rachael; Ali Jafri, Syed Rafat; Ayas, Mouhab; Jardine, Laura; Mellid, Eugenia Fernandez; Corrales, Irene; Richardson, Deborah; Özbek, Namik Yasar; Zaniewska-Tekieli, Anna; Gozdzik, Jolanta; Ryhänen, Samppa; Niinimäki, Riitta; Jahnukainen, Kirsi; Salmenniemi, Urpu; Kilpivaara, Outi; Wartiovaara-Kautto, Ulla

Long-term efficacy and safety of danicopan as add-on therapy to ravulizumab or eculizumab in PNH with significant EVH

达尼可泮作为拉武利珠单抗或依库珠单抗的附加疗法,用于治疗伴有显著EVH的阵发性睡眠性血红蛋白尿症(PNH)的长期疗效和安全性

Kulasekararaj, Austin; Griffin, Morag; Piatek, Caroline; Shammo, Jamile; Nishimura, Jun-Ichi; Patriquin, Christopher; Schrezenmeier, Hubert; Barcellini, Wilma; Panse, Jens; Gaya, Anna; Patel, Yogesh; Liu, Peng; Filippov, Gleb; Sicre de Fontbrune, Flore; Risitano, Antonio; Lee, Jong Wook

Clinical Impact of Graft Cryopreservation on Allogeneic Stem Cell Transplantation: An Italian, Registry-Based Study on Behalf of the "Gruppo Italiano Per Il Trapianto di Midollo Osseo, Cellule Staminali Emopoietiche e Terapia Cellulare" (GITMO)

移植物冷冻保存对同种异体干细胞移植的临床影响:代表“Gruppo Italiano Per Il Trapianto di Midollo Osseo, Cellule Staminali Emopietiche e Terapia Cellulare” (GITMO) 进行的意大利注册研究

Defrancesco, Irene; Ferretti, Virginia Valeria; Chiusolo, Patrizia; Russo, Domenico; Nozzoli, Chiara; Olivieri, Attilio; Gambella, Massimiliano; Cavattoni, Irene Maria; Bramanti, Stefania; Santarone, Stella; Fanin, Renato; Cairoli, Roberto; Piemontese, Simona; Parma, Matteo; Onida, Francesco; Busca, Alessandro; Castagna, Luca; Cuoghi, Angela; Pastore, Domenico; Mordini, Nicola; Benedetti, Fabio; Skert, Cristina; Borghero, Carlo; Iori, Anna Paola; Fagioli, Franca; Pavone, Vincenzo; Selleri, Carmine; Cesaro, Simone; Musso, Maurizio; Ladetto, Marco; Vallisa, Daniele; Carluccio, Paola; Picardi, Alessandra; Tozzi, Monica; Biffi, Alessandra; Milone, Giuseppe; Faraci, Maura; Prete, Arcangelo; Prezioso, Lucia; Risitano, Antonio Maria; Tambaro, Francesco Paolo; Tintori, Veronica; Galieni, Piero; Pane, Fabrizio; Zerbi, Caterina; Bianchessi, Antonio; Losi, Giulia; Romano, Francesco; Taurino, Alessia; Oldani, Elena; Polverelli, Nicola; Bonifazi, Francesca; Martino, Massimo

Long-Term Outcome of Fanconi Anemia Patients From the Italian Registry on Behalf of the Marrow Failure Study Group of the AIEOP (Italian Association for Pediatric Haematology-Oncology)

来自意大利登记处(代表意大利儿科血液肿瘤协会 (AIEOP) 骨髓衰竭研究组)的范可尼贫血患者的长期预后

Ricci, Erica; Bagnasco, Francesca; Pierri, Filomena; Risitano, Antonio; Farruggia, Piero; Faraci, Maura; Frieri, Camilla; Corti, Paola; Ramenghi, Ugo; Quarello, Paola; Barberi, Walter; Menna, Giuseppe; Giagnuolo, Giovanna; Pillon, Marta; Miano, Maurizio; Di Bartolomeo, Paolo; Santarone, Stella; Zecca, Marco; Mastrodicasa, Elena; Mura, Rosamaria; Pinazzi, Beatrice; Luti, Laura; Licciardello, Maria; Barone, Angelica; Veltroni, Marinella; Palazzi, Giovanni; Verzegnassi, Federico; Patriarca, Francesca; Onofrillo, Daniela; Cesaro, Simone; Ghilardi, Roberta; D'Alba, Irene; Angarano, Rosa; Arcuri, Luca; Beccaria, Andrea; Tallone, Ramona; Zatterale, Adriana; Dufour, Carlo

Patient-reported improvements in paroxysmal nocturnal hemoglobinuria treated with iptacopan from 2 phase 3 studies

两项 3 期研究显示,接受伊普他考潘治疗的阵发性睡眠性血红蛋白尿患者报告症状有所改善。

Risitano, Antonio M; de Castro, Carlos; Han, Bing; Kulasekararaj, Austin; Maciejewski, Jaroslaw P; Scheinberg, Phillip; Ueda, Yasutaka; Vallow, Susan; Bermann, Georgina; Dahlke, Marion; Kumar, Rakesh; Peffault de Latour, Régis

Posttransplant cyclophosphamide as GVHD prophylaxis in patients receiving mismatched unrelated HCT: the PHYLOS trial

移植后环磷酰胺作为不匹配无关供者造血干细胞移植患者移植物抗宿主病(GVHD)预防药物:PHYLOS试验

Raiola, Anna Maria; Bruno, Benedetto; Risitano, Antonio Maria; Mosna, Federico; Cavattoni, Irene Maria; Onida, Francesco; Saporiti, Giorgia; Patriarca, Francesca; Battista, Marta Lisa; Pavone, Vincenzo; Mele, Anna; Chiusolo, Patrizia; Sica, Simona; Loteta, Barbara; di Grazia, Carmen; Carella, Angelo Michele; Salvatore, Dalila; Morello, Enrico; Leoni, Alessandro; Giaccone, Luisa; Bernasconi, Paolo; Terruzzi, Elisabetta; Mordini, Nicola; Borghero, Carlo; Zallio, Francesco; Luppi, Mario; Grassi, Anna; Olivieri, Attilio; Piras, Eugenia; Sacchi, Nicoletta; Ciccone, Giovannino; Castiglione, Anna; Degrandi, Eliana; Angelucci, Emanuele; Martino, Massimo; Bonifazi, Francesca

Utilization of hematopoietic cell transplantation and cellular therapy technology in Europe and associated Countries. Using the 2022 activity survey data to correlate with economic and demographic factors. A report from the EBMT

欧洲及相关国家造血干细胞移植和细胞治疗技术的应用情况。利用2022年活动调查数据,分析其与经济和人口因素的关联性。欧洲骨髓移植协会(EBMT)报告。

Passweg, Jakob R; Baldomero, Helen; Alexander, Tobias; Angelucci, Emanuele; Averbuch, Dina; Bazarbachi, Ali; Ciceri, Fabio; Raffaella, Greco; Hazenberg, Mette D; Kalwak, Krzysztof; McLornan, Donal P; Risitano, Antonio M; Ruggeri, Annalisa; Snowden, John A; Sureda, Anna

The 2023 EBMT report on hematopoietic cell transplantation and cellular therapies. Increased use of allogeneic HCT for myeloid malignancies and of CAR-T at the expense of autologous HCT

2023年欧洲骨髓移植协会(EBMT)关于造血细胞移植和细胞疗法的报告指出,异基因造血干细胞移植(HCT)在髓系恶性肿瘤治疗中的应用日益增多,CAR-T疗法的使用也随之增加,而自体造血干细胞移植的使用则相应减少。

Passweg, Jakob R; Baldomero, Helen; Atlija, Marina; Kleovoulou, Iliana; Witaszek, Aleksandra; Alexander, Tobias; Angelucci, Emanuele; Averbuch, Dina; Bazarbachi, Ali; Ciceri, Fabio; Greco, Raffaella; Hazenberg, Mette D; Kalwak, Krzysztof; McLornan, Donal P; Neven, Bénédicte; Perić, Zinaida; Risitano, Antonio M; Ruggeri, Annalisa; Sánchez-Ortega, Isabel; Snowden, John A; Sureda, Anna