日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CCND3 Suppression Ameliorates β-Thalassaemia in a Murine Disease Model: A Potential Therapeutic Strategy

CCND3抑制可改善小鼠疾病模型中的β-地中海贫血:一种潜在的治疗策略

Caria, Cristian Antonio; Marongiu, Maria Franca; Porcu, Susanna; Poddie, Daniela; Vaccargiu, Simona; Vadolas, Jim; Meloni, Alessandra; Perseu, Lucia; Olianas, Alessandra; Ristaldi, Maria Serafina

Drugs Repurposing of Molecules Modulating Human Delta Globin Gene Expression via a Model of Transgenic Foetal Liver Cells: Implications for Beta-Hemoglobinopathy Therapeutics.

通过转基因胎肝细胞模型对调节人类δ珠蛋白基因表达的分子进行药物再利用:对β-血红蛋白病治疗的意义

Simbula Michela, Manchinu Maria Francesca, Olla Stefania, Congiu Michela, Vaccargiu Simona, Caria Cristian Antonio, Poddie Daniela, Ristaldi Maria Serafina

Post-GWAS Validation of Target Genes Associated with HbF and HbA(2) Levels

GWAS后验证与HbF和HbA(2)水平相关的靶基因

Caria, Cristian Antonio; Faà, Valeria; Porcu, Susanna; Marongiu, Maria Franca; Poddie, Daniela; Perseu, Lucia; Meloni, Alessandra; Vaccargiu, Simona; Ristaldi, Maria Serafina

miR-365-3p mediates BCL11A and SOX6 erythroid-specific coregulation: A new player in HbF activation

miR-365-3p 介导 BCL11A 和 SOX6 红细胞特异性共调节:HbF 激活中的新参与者

Michela Simbula, Maria Francesca Manchinu, Maura Mingoia, Mauro Pala, Isadora Asunis, Cristian Antonio Caria, Lucia Perseu, Manan Shah, Merlin Crossley, Paolo Moi, Maria Serafina Ristaldi

Multi-Organ Morphological Findings in a Humanized Murine Model of Sickle Cell Trait

镰状细胞性状人源化小鼠模型的多器官形态学发现

Trucas, Marcello; Burattini, Sabrina; Porcu, Susanna; Simbula, Michela; Ristaldi, Maria Serafina; Kowalik, Marta Anna; Serra, Maria Pina; Gobbi, Pietro; Battistelli, Michela; Perra, Andrea; Quartu, Marina

Deficiency in interferon type 1 receptor improves definitive erythropoiesis in Klf1 null mice

干扰素1型受体缺陷可改善Klf1基因敲除小鼠的终末红细胞生成

Manchinu, Maria Francesca; Brancia, Carla; Caria, Cristian Antonio; Musu, Ester; Porcu, Susanna; Simbula, Michela; Asunis, Isadora; Perseu, Lucia; Ristaldi, Maria Serafina

In vivo activation of the human δ-globin gene: the therapeutic potential in β-thalassemic mice

人δ-珠蛋白基因的体内激活:在β-地中海贫血小鼠中的治疗潜力

Manchinu, Maria F; Marongiu, Maria F; Poddie, Daniela; Casu, Carla; Latini, Veronica; Simbula, Michela; Galanello, Renzo; Moi, Paolo; Cao, Antonio; Porcu, Susanna; Ristaldi, Maria S

Reversible disruption of pre-pulse inhibition in hypomorphic-inducible and reversible CB1-/- mice

在低效诱导型和可逆型 CB1-/- 小鼠中,预脉冲抑制的可逆性破坏

Marongiu, Maria Franca; Poddie, Daniela; Porcu, Susanna; Manchinu, Maria Francesca; Castelli, Maria Paola; Sogos, Valeria; Bini, Valentina; Frau, Roberto; Caredda, Elisabetta; Collu, Maria; Ristaldi, Maria Serafina

Klf1 affects DNase II-alpha expression in the central macrophage of a fetal liver erythroblastic island: a non-cell-autonomous role in definitive erythropoiesis

Klf1 影响胎儿肝脏红细胞岛中央巨噬细胞中的 DNase II-alpha 表达:在确定性红细胞生成中的非细胞自主作用

Susanna Porcu, Maria F Manchinu, Maria F Marongiu, Valeria Sogos, Daniela Poddie, Isadora Asunis, Loredana Porcu, Maria G Marini, Paolo Moi, Antonio Cao, Frank Grosveld, Maria S Ristaldi

The value of some Corsican sub-populations for genetic association studies

科西嘉岛部分亚人群在遗传关联研究中的价值

Latini, Veronica; Sole, Gabriella; Varesi, Laurent; Vona, Giuseppe; Ristaldi, Maria Serafina