AAVs targeting human carbonic anhydrase IV enhance gene delivery to the brain.
靶向人类碳酸酐酶 IV 的 AAV 可增强基因向大脑的递送。
期刊:Cell Reports
影响因子:6.9
doi:10.1016/j.celrep.2025.116419
Lin Changfan, Chen Xinhong, Hoang Jonathan D, Ristic Fiona, Fan Yujie, Jang Seongmin, Chung Jin Hyung Alex, Sullivan Erin E, Gawda Tomasz, Kavvathas Bill, Tran Irene, Li Yitong, Steele Andrew D, Shay Timothy F, Gradinaru Viviana