日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A STAT3 degrader demonstrates efficacy in venetoclax resistant acute myeloid leukemia

STAT3降解剂在维奈托克耐药的急性髓系白血病中显示出疗效

Chakraborty, Samarpana; Morganti, Claudia; Zaldana, Kimberly; Rivera Pena, Bianca; Zhang, Hui; Verma, Divij; Gitego, Nadege; Ma, Feiyang; Aluri, Srinivas; Pradhan, Kith; Gordon-Mitchell, Shanisha; Mantzaris, Ioannis; Goldfinger, Mendel; Feldman, Eric; Gritsman, Kira; Shi, Yang; Hubner, Stefan; Qiu, Yi Hua; Brown, Brandon D; Khasawneh, Abdullah; Skwarska, Anna; de Camargo Magalhães, Eduardo Sabino; Verma, Amit; Konopleva, Marina; Tabe, Yoko; Gavathiotis, Evripidis; Colla, Simona; Gollob, Jared; Dey, Joyoti; Kornblau, Steven M; Koralov, Sergei B; Ito, Keisuke; Shastri, Aditi

AAV-delivered PPT1 provides long-term neurological benefits in CLN1 mice and achieves therapeutic levels in sheep brain

AAV递送的PPT1在CLN1小鼠中可提供长期的神经系统获益,并在绵羊脑中达到治疗水平。

Alam, Md Suhail; Khatiwada, Apeksha; Eaton, Samantha L; Cohen, Daniel M; White, John; Derby, Melissa; Peterson, Drew; Rivera-Pena, Graciela; Nayal, Mohamad; Becker, Mallory; Beck, Heena; Li, Charlie; Gentzel, Renee; Atkins, George; Greenhalgh, Stephen N; Lillico, Simon G; Gregson, Rachael; Clutton, Eddie; Murdoch, Fraser; Nixon, James; Gray, Mark; Thompson, Gerard; McBride, Jodi; Wishart, Thomas M; Biferi, Maria Grazia; Ramsburg, Elizabeth

ASXL1 mutations are associated with distinct epigenomic alterations that lead to sensitivity to venetoclax and azacytidine

ASXL1 突变与导致对维奈克拉和氮杂胞苷敏感性的明显表观基因组改变有关

Nora E Rahmani, Nandini Ramachandra, Srabani Sahu, Nadege Gitego, Andrea Lopez, Kith Pradhan, Tushar D Bhagat, Shanisha Gordon-Mitchell, Bianca Rivera Pena, Mohammad Kazemi, Keshav Rao, Orsi Giricz, Shahina Bano Maqbool, Raul Olea, Yongmei Zhao, Jinghang Zhang, Hamid Dolatshad, Vickram Tittrea, Dhar

Therapeutic targeting of the inflammasome in myeloid malignancies

髓系恶性肿瘤中炎症小体的治疗靶向治疗

Chakraborty, Samarpana; Shapiro, Lauren C; de Oliveira, Sofia; Rivera-Pena, Bianca; Verma, Amit; Shastri, Aditi