日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

BCMA-directed mRNA CAR T cell therapy for myasthenia gravis: a randomized, double-blind, placebo-controlled phase 2b trial

BCMA靶向mRNA CAR T细胞疗法治疗重症肌无力:一项随机、双盲、安慰剂对照的2b期试验

Vu, Tuan; Durmus, Hacer; Rivner, Michael; Shroff, Sheetal; Ragole, Thomas; Myers, Bennett; Pasnoor, Mamatha; Small, George; Karam, Chafic; Vullaganti, Mithila; Peltier, Amanda; Sahagian, Gregory; Feinberg, Marc H; Slanksy, Adam; Barnett-Tapia, Carolina; Siddiqi, Zaeem; Gwathmey, Kelly; Badruddoja, Michael A; Kamboh, Hafsa; Ruggerie, Rachel N; Fedak, Renee R; Stewart, C Andrew; Kurtoglu, Metin; Kalayoglu, Murat; Singer, Michael; Jewell, Christopher M; Miljkovic, Milos D; Dimachkie, Mazen; Mozaffar, Tahseen; Howard, James F Jr

Multicenter Expanded Access Protocol for Research Through Access to Trehalose in People With Amyotrophic Lateral Sclerosis

通过获取海藻糖,为肌萎缩侧索硬化症患者开展研究的多中心扩大使用方案

Krivickas, Brooke; Scirocco, Erica; Giacomelli, Elisa; Sharma, Saloni; Benson, Molly; Keegan, Mackenzie; Kulesa-Kelley, Jennifer; Chibnik, Lori B; Casagrande, Gabriella; Heyd, Lindsay; Chase, Marianne; Drake, Kristin; Mohapatra, Silpa; Hagar, Jennifer Linn; Hasenoehrl, Meredith Gibbons; Dagostino, Derek; Sherman, Alexander V; Leite, Alex; Yu, Hong; Rosenthal, Jesse; Miller, Timothy; McCaffrey, Alexandra; Gwathmey, Kelly; Locatelli, Eduardo; Bayat, Elham; Heitzman, Daragh; Young, Eufrosina; Goyal, Namita A; Whitesell, Jackie; Felice, Kevin; Ilieva, Hristelina; Swenson, Andrea; Walk, David; Alameda, Gustavo; Foster, Laura; McIlduff, Courtney E; Walsh, Alison; Zilliox, Lindsay; Ajroud-Driss, Senda; Bodkin, Cynthia; Katz, Jonathan; Ladha, Shafeeq; Rivner, Michael; Rosow, Laura; Twydell, Paul; Wasiewski, Warren; Babu, Suma; Berry, James D; Paganoni, Sabrina

Efficacy and safety of maintenance intravenous immunoglobulin in generalized myasthenia gravis patients with acetylcholine receptor antibodies: A multicenter, double-blind, placebo-controlled trial

维持性静脉注射免疫球蛋白治疗伴有乙酰胆碱受体抗体的全身型重症肌无力患者的疗效和安全性:一项多中心、双盲、安慰剂对照试验

Bril, Vera; Berkowicz, Tomasz; Szczudlik, Andrzej; Nicolle, Michael W; Bednarik, Josef; Hon, Petr; Vaitkus, Antanas; Vu, Tuan; Rozsa, Csilla; Magnus, Tim; Panczel, Gyula; Toomsoo, Toomas; Pasnoor, Mamatha; Mozaffar, Tahseen; Freimer, Miriam; Reuner, Ulrike; Vécsei, László; Souayah, Nizar; Levine, Todd; Pascuzzi, Robert M; Dalakas, Marinos C; Rivner, Michael; Griffin, Rhonda; Coll, Montse Querolt; Mondou, Elsa

Safety and tolerability of tegoprubart in patients with amyotrophic lateral sclerosis: A Phase 2A clinical trial.

替戈普鲁巴特治疗肌萎缩侧索硬化症患者的安全性和耐受性:一项 2A 期临床试验

Perrin Steven, Ladha Shafeeq, Maragakis Nicholas, Rivner Michael H, Katz Jonathan, Genge Angela, Olney Nicholas, Lange Dale, Heitzman Daragh, Bodkin Cynthia, Jawdat Omar, Goyal Namita A, Bornstein Jeffrey D, Mak Carmen, Appel Stanley H, Paganoni Sabrina

Efficacy, safety and tolerability of rozanolixizumab in patients with chronic inflammatory demyelinating polyradiculoneuropathy: a randomised, subject-blind, investigator-blind, placebo-controlled, phase 2a trial and open-label extension study

罗扎诺利珠单抗对慢性炎症性脱髓鞘性多发性神经根神经病患者的疗效、安全性和耐受性:一项随机、受试者盲法、研究者盲法、安慰剂对照、 2a 期试验和开放标签扩展研究

Luis Querol, Jérôme De Sèze, Tina Dysgaard, Todd Levine, T Hemanth Rao, Michael Rivner, Hans-Peter Hartung, Peter Kiessling, Saori Shimizu, Dominika Marmol, Ali Bozorg, Anny-Odile Colson, Ute Massow, Filip Eftimov; CIDP01 Study Investigators

Randomized Double-Blind Placebo-Controlled Trial of the Corticosteroid-Sparing Effects of Immunoglobulin in Myasthenia Gravis

免疫球蛋白在重症肌无力中减少皮质类固醇用量的随机双盲安慰剂对照试验

Bril, Vera; Szczudlik, Andrzej; Vaitkus, Antanas; Rozsa, Csilla; Kostera-Pruszczyk, Anna; Hon, Petr; Bednarik, Josef; Tyblova, Michaela; Köhler, Wolfgang; Toomsoo, Toomas; Nowak, Richard J; Mozaffar, Tahseen; Freimer, Miriam L; Nicolle, Michael W; Magnus, Tim; Pulley, Michael T; Rivner, Michael; Dimachkie, Mazen M; Distad, B Jane; Pascuzzi, Robert M; Babiar, Donna; Lin, Jiang; Querolt Coll, Montse; Griffin, Rhonda; Mondou, Elsa

Effect of Ezogabine on Cortical and Spinal Motor Neuron Excitability in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial

依佐加宾对肌萎缩侧索硬化症皮质和脊髓运动神经元兴奋性的影响:一项随机临床试验

Wainger, Brian J; Macklin, Eric A; Vucic, Steve; McIlduff, Courtney E; Paganoni, Sabrina; Maragakis, Nicholas J; Bedlack, Richard; Goyal, Namita A; Rutkove, Seward B; Lange, Dale J; Rivner, Michael H; Goutman, Stephen A; Ladha, Shafeeq S; Mauricio, Elizabeth A; Baloh, Robert H; Simmons, Zachary; Pothier, Lindsay; Kassis, Sylvia Baedorf; La, Thuong; Hall, Meghan; Evora, Armineuza; Klements, David; Hurtado, Aura; Pereira, Joao D; Koh, Joan; Celnik, Pablo A; Chaudhry, Vinay; Gable, Karissa; Juel, Vern C; Phielipp, Nicolas; Marei, Adel; Rosenquist, Peter; Meehan, Sean; Oskarsson, Björn; Lewis, Richard A; Kaur, Divpreet; Kiskinis, Evangelos; Woolf, Clifford J; Eggan, Kevin; Weiss, Michael D; Berry, James D; David, William S; Davila-Perez, Paula; Camprodon, Joan A; Pascual-Leone, Alvaro; Kiernan, Matthew C; Shefner, Jeremy M; Atassi, Nazem; Cudkowicz, Merit E

Characterization of LRP4/Agrin Antibodies From a Patient With Myasthenia Gravis

重症肌无力患者 LRP4/Agrin 抗体的表征

Zheng Yu, Meiying Zhang, Hongyang Jing, Peng Chen, Rangjuan Cao, Jinxiu Pan, Bin Luo, Yue Yu, Brandy M Quarles, Wencheng Xiong, Michael H Rivner, Lin Mei

Effects of mexiletine on hyperexcitability in sporadic amyotrophic lateral sclerosis: Preliminary findings from a small phase II randomized controlled trial

美西律对散发性肌萎缩侧索硬化症患者过度兴奋的影响:一项小型 II 期随机对照试验的初步结果

Weiss, Michael D; Macklin, Eric A; McIlduff, Courtney E; Vucic, Steve; Wainger, Brian J; Kiernan, Matthew C; Goutman, Stephen A; Goyal, Namita A; Rutkove, Seward B; Ladha, Shafeeq S; Chen, I-Hweii Amy; Harms, Matthew B; Brannagan, Thomas H; Lacomis, David; Zivkovic, Sasha; Ma, Maxwell; Wang, Leo H; Simmons, Zachary; Rivner, Michael H; Shefner, Jeremy M; Cudkowicz, Merit E; Atassi, Nazem

Flecainide Toxicity Leading to Loss of Pacemaker Capture and Cardiac Arrest

氟卡尼中毒导致起搏器失控和心脏骤停

Rivner, Harold; Lambrakos, Litsa K