Single-dose genome editing therapy rescues auditory and vestibular functions in adult mice with DFNA41 deafness
单剂量基因编辑疗法可挽救患有 DFNA41 耳聋的成年小鼠的听觉和前庭功能
期刊:Journal of Clinical Investigation
影响因子:13.6
doi:10.1172/JCI187872
Wei, Wei; Zhu, Wenliang; Silver, Stewart; Armstrong, Ariel M; Robbins, Fletcher S; Rameshbabu, Arun Prabhu; Walz, Katherina; Quan, Yizhou; Du, Wan; Kim, Yehree; Indzhykulian, Artur A; Shu, Yilai; Liu, Xue-Zhong; Chen, Zheng-Yi