CRISPR/Cas9 generated knockout mice lacking phenylalanine hydroxylase protein as a novel preclinical model for human phenylketonuria
CRISPR/Cas9 生成缺乏苯丙氨酸羟化酶蛋白的敲除小鼠，作为人类苯丙酮尿症的新型临床前模型
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-021-86663-8
Kuldeep Singh, Cathleen S Cornell, Robert Jackson, Mostafa Kabiri, Michael Phipps, Mitul Desai, Robert Fogle, Xiaoyou Ying, Gulbenk Anarat-Cappillino, Sarah Geller, Jennifer Johnson, Errin Roberts, Katie Malley, Tim Devlin, Matthew DeRiso, Patricia Berthelette, Yao V Zhang, Susan Ryan, Srinivas Rao,
