Activation of autophagy reverses progressive and deleterious protein aggregation in PRPF31 patient-induced pluripotent stem cell-derived retinal pigment epithelium cells
自噬激活可逆转 PRPF31 患者诱导的多能干细胞来源的视网膜色素上皮细胞中进行性和有害的蛋白质聚集
期刊:Clinical and Translational Medicine
影响因子:7.9
doi:10.1002/ctm2.759
Maria Georgiou, Chunbo Yang, Robert Atkinson, Kuan-Ting Pan, Adriana Buskin, Marina Moya Molina, Joseph Collin, Jumana Al-Aama, Franziska Goertler, Sebastian E J Ludwig, Tracey Davey, Reinhard Lührmann, Sushma Nagaraja-Grellscheid, Colin A Johnson, Robin Ali, Lyle Armstrong, Viktor Korolchuk, Hennin