Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease
庞贝病鞘内基因治疗的长期神经和心脏矫正
期刊:Acta Neuropathologica Communications
影响因子:6.2
doi:10.1186/s40478-017-0464-2
J Hordeaux, L Dubreil, C Robveille, J Deniaud, Q Pascal, B Dequéant, J Pailloux, L Lagalice, M Ledevin, C Babarit, P Costiou, F Jamme, M Fusellier, Y Mallem, C Ciron, C Huchet, C Caillaud, M-A Colle