Systematic deletion of symmetrical CFTR exons reveals new therapeutic targets for exon skipping antisense oligonucleotides
系统性删除对称性CFTR外显子揭示了外显子跳跃反义寡核苷酸的新治疗靶点
期刊:
影响因子:
doi:10.1093/narmme/ugae017
Pena-Rasgado, Cecilia; Rodriguez-Manriquez, Elvia; Dundr, Miroslav; Bridges, Robert J; Hastings, Michelle L; Michaels, Wren E
