日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Measuring What Matters to Patients with Pompe Disease: A Review of Clinical Outcome Assessments for Capturing Treatment Benefits of Innovative Novel Therapies

衡量庞贝病患者真正关心的指标：创新疗法治疗获益的临床结果评估综述

期刊:Advances in Therapy
影响因子:
doi:10.1007/s12325-025-03483-2
Rofail, Diana; Ginchereau Sowell, France; Williams, Betsy; Patel, Nick; Karantzoulis, Stella; Avbersek, Andreja
发表日期：2026
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Advancing Future Amyotrophic Lateral Sclerosis Medicines by Incorporating The Patient Voice Into Patient-Centered Holistic Measurement Strategies for Clinical and Real-World Studies: Results from Targeted Literature Reviews

通过将患者的声音融入以患者为中心的整体测量策略，推进肌萎缩侧索硬化症的未来药物研发，以开展临床和真实世界研究：来自针对性文献综述的结果

期刊:Neurology and Therapy
影响因子:4.8
doi:10.1007/s40120-025-00740-y
Rofail, Diana; Chladek, Michael; Williams, Betsy; Patel, Nick; Nowell, William B; Karantzoulis, Stella; Levy, Oren
发表日期：2025
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Safety, Efficacy, and Patient-Reported Outcomes From a Phase 2 Randomized Trial of Pozelimab and Cemdisiran Combination in Patients With Paroxysmal Nocturnal Hemoglobinuria

一项评估波泽利单抗和西美沙酮联合治疗阵发性睡眠性血红蛋白尿患者的 II 期随机试验的安全性、有效性和患者报告结局

期刊:eJHaem
影响因子:1.2
doi:10.1002/jha2.70095
Jang, Jun-Ho; Wong, Raymond Siu Ming; Hartford, Christopher; Pavani, Rodrigo; Aurand, Lisa; Nguyen, Quang; Mohan, Kosalai; Meagher, Karoline; Sherman, Steven; Rofail, Diana; Perlee, Lorah; Souttou, Amal; Kelly, Richard J
发表日期：2025
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PFAS Exposure, Mental Health, and Environmental Justice in the United States: Impacts on Marginalized Communities

美国 PFAS 暴露、心理健康和环境正义：对边缘化群体的影响

期刊:International Journal of Environmental Research and Public Health
影响因子:
doi:10.3390/ijerph22071116
Sukhram, Shiryn D; Kim, Ji; Musovic, Sabrina; Anidugbe, Ayotunde; Corte, Emiliano; Ahsan, Tasneem; Rofail, Selvia; Mesquita, Nicolli; Padilla, Miguel
FAS
发表日期：2025
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Patient-Reported Outcomes in COVID-19 Treatment with Monoclonal Antibodies Reveal Benefits in Return to Usual Activities

患者报告的COVID-19单克隆抗体治疗结果显示，恢复正常活动具有益处

期刊:Infectious Diseases and Therapy
影响因子:5.3
doi:10.1007/s40121-024-01013-1
Rofail, Diana; Hussein, Mohamed; Naumann, Ulrike; Podolanczuk, Anna J; Norton, Thomas; Ali, Shazia; Mastey, Vera; Ivanescu, Cristina; Hirshberg, Boaz; Geba, Gregory P
单克隆抗体
发表日期：2024
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A Patient-Relevant Measurement Strategy to Assess Clinical Benefit of Novel Therapies for Non-metastatic Cutaneous Squamous Cell Carcinoma

评估新型疗法对非转移性皮肤鳞状细胞癌临床获益的患者相关测量策略

期刊:Oncology and Therapy
影响因子:3.2
doi:10.1007/s40487-024-00304-4
Rofail, Diana; Ciesluk, Anna; Lovell, Teya; Marquis, Patrick; Fury, Matthew G; Chen, Chieh-I
细胞生物学
肿瘤
肿瘤免疫
发表日期：2024
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The symptoms evolution of long COVID‑19 (SE-LC19): a new patient-reported content valid instrument

新冠肺炎长期症状演变（SE-LC19）：一种新的患者自评内容效度良好的工具

期刊:Journal of Patient-Reported Outcomes
影响因子:2.9
doi:10.1186/s41687-024-00737-5
Rofail, Diana; Somersan-Karakaya, Selin; Mylonakis, Eleftherios; Choi, Julia Y; Przydzial, Krystian; Marquis, Sarah; Zhao, Yuming; Hussein, Mohamed; Norton, Thomas D; Podolanczuk, Anna J; Geba, Gregory P
肺炎
新冠
微生物学
发表日期：2024
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Glucose-6-phosphate dehydrogenase deficiency and neonatal indirect hyperbilirubinemia: a retrospective cohort study among 40,305 consecutively born babies

葡萄糖-6-磷酸脱氢酶缺乏症与新生儿间接高胆红素血症：一项对40305名连续出生婴儿的回顾性队列研究

期刊:Journal of Perinatology
影响因子:2.4
doi:10.1038/s41372-024-01927-1
Al-Bedaywi, Rajai Rofail Raja; Salameh, Khalil Mohd Khalil; Abedin, Sarfrazul; Viswanathan, Brijroy; Khedr, Abedalkhalik Ahmad; Habboub, Lina Hussain M
发表日期：2024
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Thematic analysis to explore patients' experiences with long COVID-19: a conceptual model of symptoms and impacts on daily lives

运用主题分析法探索新冠肺炎长期症状患者的经历：症状及其对日常生活影响的概念模型

期刊:BMJ Open
影响因子:2.3
doi:10.1136/bmjopen-2023-076992
Rofail, Diana; Somersan-Karakaya, Selin; Choi, Julia Y; Przydzial, Krystian; Zhao, Yuming; Hussein, Mohamed; Norton, Thomas D; Podolanczuk, Anna J; Mylonakis, Eleftherios; Geba, Gregory P
肺炎
新冠
微生物学
发表日期：2024
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Experience of Daily Life with Generalized Myasthenia Gravis: A Qualitative Investigation and Assessment of Instrument Content Validity

重症肌无力患者日常生活体验：一项定性调查和工具内容效度评估

期刊:Neurology and Therapy
影响因子:4.8
doi:10.1007/s40120-023-00544-y
Hartford, Christopher A; Sherman, Steven A; Karantzoulis, Stella; Guillemin, Isabelle; Phinney, Michael G; Kelly, Kimberly L; Negron, Kayla E; Raja, Shruti M; Rofail, Diana
重症肌无力
免疫/内分泌
发表日期：2023
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