Targeted correction of a thalassemia-associated beta-globin mutation induced by pseudo-complementary peptide nucleic acids
利用假互补肽核酸靶向纠正地中海贫血相关β-珠蛋白突变
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkp217
Lonkar, Pallavi; Kim, Ki-Hyun; Kuan, Jean Y; Chin, Joanna Y; Rogers, Faye A; Knauert, Melissa P; Kole, Ryszard; Nielsen, Peter E; Glazer, Peter M