Irradiation- and busulfan-free stem cell transplantation in Fanconi anemia using an anti-CD117 antibody: a phase 1b trial
使用抗CD117抗体治疗范可尼贫血的无辐射、无白消安干细胞移植：一项1b期试验
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-025-03817-1
Agarwal, Rajni; Bertaina, Alice; Soco, Charmaine; Long-Boyle, Janel R; Saini, Gopin; Kunte, Nivedita; Hiroshima, Lyndsie; Chan, Yan Y; Willner, Hana; Krampf, Mark R; Nofal, Rofida; Barbarito, Giulia; Sen, Sushmita; Van Hentenryck, Maite; Walck, Emily; Scheck, Amelia; Perriman, Rhonda J; Bouge, Alisha; Istomina, Elena; Din, Hena Naz; Klinger, Edna F; Cheng, Jerry C; Wlodarski, Marcin W; Boelens, Jaap J; Shizuru, Judith A; Pang, Wendy W; Weinberg, Kenneth; Parkman, Robertson; Roncarolo, Maria Grazia; Porteus, Matthew; Czechowicz, Agnieszka
