日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Mapping VEXAS-associated and rare UBA1 variants in the United Kingdom: Insights from patient cohorts and the general population

英国VEXAS相关及罕见UBA1变异的分布图谱:来自患者队列和普通人群的启示

Martinez Rodriguez, Ana; Chang, Leon; Rowczenio, Dorota; Smith, Alexandra; Omoyinmi, Ebun; Poulter, James A; McGregor, Andrew; Francis, Sebastian; Trikha, Roochi; Al-Hakim, Adam; Lok Kong, Kar; Kent, David G; Lachmann, Helen; Kulasekararaj, Austin; Cargo, Catherine; Savic, Sinisa

Hypomethylating agents in vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic syndrome (VEXAS): A systematic review

空泡低甲基化剂、E1酶、X连锁自身炎症性体细胞综合征(VEXAS):系统评价

Hoff, Fieke W; Trikha, Roochi; Groarke, Emma M; Patel, Bhavisha A

Paroxysmal Nocturnal Haemoglobinuria-Associated Acute Cutaneous Thrombosis and Haemolysis in the Setting of Parvovirus B19 and Varicella Zoster Virus Infection

阵发性睡眠性血红蛋白尿症相关急性皮肤血栓形成和溶血,发生于细小病毒B19和水痘-带状疱疹病毒感染背景下

Potter, Louise J; Trikha, Roochi; Gandhi, Shreyans; Large, Joanne; Basu, Tanya N; Boissiere, Jeanne; Devine, Hannah; Sugai, Taku; Rasool, Aushna; Kulasekararaj, Austin

Characterization of Breakthrough Hemolysis in Patients With Paroxysmal Nocturnal Hemoglobinuria: An International Multicenter Experience

阵发性睡眠性血红蛋白尿患者突破性溶血的特征:一项国际多中心研究

Fattizzo, Bruno; Pedone, Giacinto Luca; Metafuni, Elisabetta; Beggiato, Eloise; Giai, Valentina; Natalie Oliva, Esther; Ricchiuti, Antony; Bortolotti, Marta; Raso, Simona; Carlino, Daniela; Memoli, Mara; Vecchi, Sofia; Vidler, Jennifer; Gogoi, Sukanya; Goel, Shreya; Corby, Anna; Trikha, Roochi; Balakrishnan, Sneha; Passamonti, Francesco; Paola Iori, Anna; Sica, Simona; Gandhi, Shreyans; Barcellini, Wilma; Kulasekararaj, Austin

Elderly Patients With Aplastic Anemia: Treatment Patterns and Outcomes in the Real World

老年再生障碍性贫血患者:真实世界中的治疗模式和结果

Fattizzo, Bruno; Gurnari, Carmelo; Giammarco, Sabrina; Ricchiuti, Antony; Awada, Hussein; Bortolotti, Marta; Galli, Nicole; Pedone, Giacinto Luca; Versino, Francesco; Consonni, Dario; Trikha, Roochi; Gandhi, Shreyans; Sica, Simona; Maciejewski, Jaroslaw P; Kulasekararaj, Austin; Barcellini, Wilma

Terminal complement inhibition and control of hemolysis in patients with paroxysmal nocturnal hemoglobinuria who switched from high-dose eculizumab to ravulizumab: a phase IV, single-arm clinical trial

在阵发性睡眠性血红蛋白尿症患者中,从高剂量依库珠单抗换用拉武珠单抗后,末端补体抑制和溶血控制:一项IV期单臂临床试验

Griffin, Morag; Gandhi, Shreyans; Kelly, Richard J; Munir, Talha; Trikha, Roochi; Hicks, Eden; Jain, Deepak; Ogawa, Masayo; Yu, Ji; Muus, Petra; Kulasekararaj, Austin G

Examining Consistency Across NICE Single Technology Appraisals: A Review of Appraisals for Paroxysmal Nocturnal Haemoglobinuria

考察NICE单一技术评估的一致性:阵发性睡眠性血红蛋白尿症评估综述

Donoghue, Jeremiah; Youngs, Matthew; Reeve, Alex; Vydyula, Krishna; Kunst, Natalia; Trikha, Roochi; Gallacher, Daniel

De-escalation of corticosteroids and clonal remission in UBA1 mutation-driven VEXAS syndrome with 5-azacytidine

5-氮胞苷治疗UBA1突变驱动的VEXAS综合征可降低皮质类固醇用量并实现克隆缓解

Trikha, Roochi; Kong, Kar Lok; Galloway, James; Basu, Tanya N; Quek, Lynn; Wilson, Jamie; Gamble, Louise; Wong, Henna; Best, Steven; Kulasekararaj, Austin

Deciphering treatment patterns in non-severe/moderate aplastic anemia: an international observational study

解读非重度/中度再生障碍性贫血的治疗模式:一项国际观察性研究

Fattizzo, Bruno; Gurnari, Carmelo; Cassanello, Giulio; Bortolotti, Marta; Awada, Hussein; Giammarco, Sabrina; Consonni, Dario; Sica, Simona; Gandhi, Shreyans; Trikha, Roochi; Large, Joanna; Salter, Sarah; Maciejewski, Jaroslaw P; Barcellini, Wilma; Kulasekararaj, Austin G

The Effect of Respiratory Viral Infections on Breakthrough Hemolysis in Patients with Paroxysmal Nocturnal Hemoglobinuria

呼吸道病毒感染对阵发性睡眠性血红蛋白尿患者突破性溶血的影响

Lazana, Ioanna; Apap Mangion, Sean; Babiker, Selma; Large, Joanna; Trikha, Roochi; Zuckerman, Mark; Gandhi, Shreyans; Kulasekararaj, Austin G