Early spinal muscular atrophy treatment following newborn screening: A 20-month review of the first Italian regional experience
新生儿筛查后的早期脊髓性肌萎缩症治疗:意大利地区首次经验的 20 个月回顾
期刊:Annals of Clinical and Translational Neurology
影响因子:4.4
doi:10.1002/acn3.52018
Delia Gagliardi, Eleonora Canzio, Paola Orsini, Pasquale Conti, Vita Sinisi, Cosimo Maggiore, Maria Carla Santarsia, Giuseppina Lagioia, Giovanna Lupis, Isabella Roppa, Gaetano Scianatico, Daniela Mancini, Stefania Corti, Giacomo Pietro Comi, Mattia Gentile #, Delio Gagliardi #