Biochemical Studies on Human Ornithine Aminotransferase Support a Cell-Based Enzyme Replacement Therapy in the Gyrate Atrophy of the Choroid and Retina
人鸟氨酸氨基转移酶的生化研究支持基于细胞的酶替代疗法用于治疗脉络膜和视网膜回旋状萎缩。
期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms25147931
Pampalone, Gioena; Chiasserini, Davide; Pierigè, Francesca; Camaioni, Emidio; Orvietani, Pier Luigi; Bregalda, Alessandro; Menotta, Michele; Bellezza, Ilaria; Rossi, Luigia; Cellini, Barbara; Magnani, Mauro