日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Ex vivo long-term expansion of human hematopoietic stem and progenitor cells as a tool for modeling vector integration sites and clonality.

体外长期扩增人类造血干细胞和祖细胞作为模拟载体整合位点和克隆性的工具。

Fleischauer Jenni, John-Neek Philipp, Ha Teng-Cheong, Mansel Friederike, Kosanke Maike, Selich Anton, Hagedorn Maike, Bastone Antonella Lucía, Schinke Maximilian, Dziadek Violetta, Dittrich-Breiholz Oliver, von Kaisenberg Constantin, Schambach Axel, Rothe Michael

Pharmacological and pre-clinical safety profile of rSIV.F/HN, a hybrid lentiviral vector for cystic fibrosis gene therapy

rSIV.F/HN(一种用于囊性纤维化基因治疗的混合慢病毒载体)的药理学和临床前安全性概况

Moiseenko, Alena; Sinadinos, Anthony; Sergijenko, Ana; Pineault, Kyriel; Saleh, Aarash; Nekola, Konradin; Strang, Nathalie; Eleftheraki, Anastasia; Boyd, A Christopher; Davies, Jane C; Gill, Deborah R; Hyde, Stephen C; McLachlan, Gerry; Rath, Tim; Rothe, Michael; Schambach, Axel; Hobbie, Silke; Schuler, Michael; Maier, Udo; Thomas, Matthew J; Mennerich, Detlev; Schmidt, Manfred; Griesenbach, Uta; Alton, Eric W F W; Kreuz, Sebastian

IFN-γ-Induced CD317 Tethers Extracellular Vesicles to Mesenchymal Stromal Cells Interfering With Immune Modulation.

IFN-γ诱导的CD317将细胞外囊泡锚定到间充质基质细胞上,从而干扰免疫调节

Selich Anton, Weisskoeppel Luisa, Hass Ralf, Hegermann Jan, Schwarzer Adrian, von Kaisenberg Constantin, Schambach Axel, Rothe Michael

Safety and efficacy of gene therapy for RAG1-deficient SCID

RAG1缺陷型重症联合免疫缺陷症基因治疗的安全性和有效性

Staal, Frank J T; Pike-Overzet, Karin; de Kivit, Sander; Ott de Bruin, Lisa; Mamede, Lucia; Pergent, Martine; Prevot, Johan; Rothe, Michael; Schambach, Axel; Lankester, Arjan

Pilocytic astrocytoma in a child with spinal muscular atrophy treated with onasemnogene abeparvovec

一名接受onasemnogene abeparvovec治疗的脊髓性肌萎缩症患儿出现毛细胞型星形细胞瘤。

Holzwarth, Dorothea; Calaminus, Gabriele; Friese, Johannes; Sejersen, Thomas; Büning, Hildegard; John-Neek, Philipp; Bastone, Antonella Lucía; Rothe, Michael; Mansfield, Keith; Libertini, Silvana; Dubost, Valérie; Kuzmiski, Brent; Alecu, Iulian; Labik, Ivan; Kirschner, Janbernd

In-Line Combustion System for the Measurement of δ(13)C-CH(4) in Gas Reference Materials Using Optical Isotope Ratio Spectroscopy

利用光学同位素比光谱法测量气体参考物质中δ(13)C-CH(4)的在线燃烧系统

Hillier, Aimee; Mussell-Webber, Eric; Hopkinson, Emily; Wilson, Freya; Nehrbass-Ahles, Christoph; Brewer, Paul J; Worton, David R; Rennick, Christopher; Arnold, Tim; Moossen, Heiko; Rothe, Michael; Geilmann, Heike; Dylag, Caroline; Hill-Pearce, Ruth E

Technical recommendations for analyzing oxylipins by liquid chromatography-mass spectrometry

利用液相色谱-质谱法分析氧化脂质的技术建议

Schebb, Nils Helge; Kampschulte, Nadja; Hagn, Gerhard; Plitzko, Kathrin; Meckelmann, Sven W; Ghosh, Soumita; Joshi, Robin; Kuligowski, Julia; Vuckovic, Dajana; Botana, Marina T; Sánchez-Illana, Ángel; Zandkarimi, Fereshteh; Das, Aditi; Yang, Jun; Schmidt, Louis; Checa, Antonio; Roche, Helen M; Armando, Aaron M; Edin, Matthew L; Lih, Fred B; Aristizabal-Henao, Juan J; Miyamoto, Sayuri; Giuffrida, Francesca; Moussaieff, Arieh; Domingues, Rosário; Rothe, Michael; Hinz, Christine; Das, Ujjalkumar Subhash; Rund, Katharina M; Taha, Ameer Y; Hofstetter, Robert K; Werner, Markus; Werz, Oliver; Kahnt, Astrid S; Bertrand-Michel, Justine; Le Faouder, Pauline; Gurke, Robert; Thomas, Dominique; Torta, Federico; Milic, Ivana; Dias, Irundika H K; Spickett, Corinne M; Biagini, Denise; Lomonaco, Tommaso; Idborg, Helena; Liu, Jun-Yan; Fedorova, Maria; Ford, David A; Barden, Anne; Mori, Trevor A; Kennedy, Paul D; Maxey, Kirk; Ivanisevic, Julijana; Gallart-Ayala, Hector; Gladine, Cécile; Wenk, Markus; Galano, Jean-Marie; Durand, Thierry; Stark, Ken D; Barbas, Coral; Garscha, Ulrike; Gelhaus, Stacy L; Ceglarek, Uta; Flamand, Nicolas; Griffin, Julian L; Ahrends, Robert; Arita, Makoto; Zeldin, Darryl C; Schopfer, Francisco J; Quehenberger, Oswald; Julian, Randall; Nicolaou, Anna; Blair, Ian A; Murphy, Michael P; Hammock, Bruce D; Freeman, Bruce; Liebisch, Gerhard; Serhan, Charles N; Köfeler, Harald C; Jakobsson, Per-Johan; Steinhilber, Dieter; Gelb, Michael H; Holčapek, Michal; Andrew, Ruth; Giera, Martin; FitzGerald, Garret A; Murphy, Robert C; Newman, John W; Dennis, Edward A; Ekroos, Kim; Milne, Ginger L; Gijón, Miguel A; Vesper, Hubert W; Wheelock, Craig E; O'Donnell, Valerie B

EXTH-50. Development of EGFR/IL13Ra2 bispecific CAR T cells to overcome heterogeneous glioblastoma

EXTH-50. 开发EGFR/IL13Ra2双特异性CAR T细胞以克服胶质母细胞瘤的异质性

Alghamdi, Fadi Ali; Alotaibi, Yaser Omar; Alshehri, Sumayah Dhafer; Zahrani, Anhar Khalid; Alhawsawi, Waseem Khalid; Alzaidi, Reema Saeed; Bondagji, Mohammed Fuad; Niyazi, Ahmed Abdulshakur; Du, Kaixin; Villasenor, Yolanda; Machuca, Robert; Trac, Candi; Park, Miso; Ma, Eric; Masia, Christian; Rothe, Michael; Jewel, Yead; Williams, John; Brown, Christine

Prdm16 mutation determines sex-specific cardiac metabolism and identifies two novel cardiac metabolic regulators

Prdm16 突变决定性别特异性心脏代谢,并鉴定出两种新的心脏代谢调节因子。

Kühnisch, Jirko; Theisen, Simon; Dartsch, Josephine; Fritsche-Guenther, Raphaela; Kirchner, Marieluise; Obermayer, Benedikt; Bauer, Anna; Kahlert, Anne-Karin; Rothe, Michael; Beule, Dieter; Heuser, Arnd; Mertins, Philipp; Kirwan, Jennifer A; Berndt, Nikolaus; MacRae, Calum A; Hubner, Norbert; Klaassen, Sabine

Preclinical lentiviral hematopoietic stem cell gene therapy corrects Pompe disease-related muscle and neurological manifestations.

临床前慢病毒造血干细胞基因疗法可纠正庞贝病相关的肌肉和神经系统症状

Yoon John K, Schindler Jeffrey W, Loperfido Mariana, Baricordi Cristina, DeAndrade Mark P, Jacobs Mary E, Treleaven Christopher, Plasschaert Robert N, Yan Aimin, Barese Cecilia N, Dogan Yildirim, Chen Vicky Ping, Fiorini Claudia, Hull Fritz, Barbarossa Luigi, Unnisa Zeenath, Ivanov Daniel, Kutner Robert H, Guda Swaroopa, Oborski Christine, Maiwald Tim, Michaud Véronique, Rothe Michael, Schambach Axel, Pfeifer Richard, Mason Chris, Biasco Luca, van Til Niek P