日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Spatial profiling of gene editing by in situ sequencing in mice and macaques

利用原位测序技术对小鼠和猕猴的基因编辑进行空间分析

Janjuha, Sharan; Haenggi, Tatjana; Chamberlain, Thomas C; Rothgangl, Tanja; Kissling, Lucas; Wilhelm, Maria; Mathis, Nicolas; Boeck, Desiree; Marquart, Kim; Ioannidi, Eleonora; Moon, Woohyun J; Muramatsu, Hiromi; Vadovics, Máté; Pardi, Norbert; Semple, Sean C; Tam, Ying K; Schwank, Gerald

Prime editing of the β(1) adrenoceptor in the brain restores physiological REM sleep in a mouse model of Alzheimer's disease.

对大脑中β(1)肾上腺素受体进行原始编辑,可恢复阿尔茨海默病小鼠模型的生理性快速眼动睡眠。

Böck Desirée, Tidecks Lisa, Wilhelm Maria, ElGrawani Waleed, Duss Sian, Trevisan Chiara, Vena Dalila, Reuss Anna Maria, Kissling Lucas, Ranucci Matteo, Privitera Mattia, Polzer Lisa K, Economides Athena E, Ioannidi Eleonora I, Mendes Raquel, Weber Yanik, Leonardi Justine, Mumenthaler Jonas, Villiger Elina, Goutagny Romain, Mathis Chantal, Schmidheini Lukas, Rothgangl Tanja, Janjuha Sharan, Patriarchi Tommaso, Bohacek Johannes, Sych Yaroslav, Aguzzi Adriano, Winterer Jochen, Kompotis Konstantinos, Schwank Gerald

Cell-stereotyped DNA repair outcomes are widespread during genome editing

在基因组编辑过程中,细胞刻板的DNA修复结果普遍存在。

Schlapansky, Moritz F; Schröder, Markus S; Santinha, Antonio J; Rothgangl, Tanja; Ioannidi, Eleonora I; Cullot, Grégoire; Lewkow, Bohdan; Ortega, German Camargo; Nouraiz, Ahmed; Mailänder, Dominic; Selbert, Louisa; Lam, Simon; Egea, Aitana; Shin, Jiyung J; Bordi, Matteo; DeWitt, Mark; Gvozdenovic, Ana; Jackson, Stephen P; Schroeder, Timm; Gehart, Helmuth; Schwank, Gerald; Platt, Randall J; Corn, Jacob E

Effective genome editing with an enhanced ISDra2 TnpB system and deep learning-predicted ωRNAs.

利用增强型 ISDra2 TnpB 系统和深度学习预测的 αRNA 进行有效的基因组编辑

Marquart Kim Fabiano, Mathis Nicolas, Mollaysa Amina, Müller Saphira, Kissling Lucas, Rothgangl Tanja, Schmidheini Lukas, Kulcsár Péter István, Allam Ahmed, Kaufmann Masako M, Matsushita Mai, Haenggi Tatjana, Cathomen Toni, Kopf Manfred, Krauthammer Michael, Schwank Gerald

Therapeutic liver cell transplantation to treat murine PKU

利用肝细胞移植治疗小鼠苯丙酮尿症

Willimann, Melanie; Grisch-Chan, Hiu Man; Rimann, Nicole; Rothgangl, Tanja; Hruzova, Martina; Schwank, Gerald; Thöny, Beat

In vivo targeting of a variant causing vanishing white matter using CRISPR/Cas9.

利用 CRISPR/Cas9 技术在体内靶向导致白质消失的变异体

Hillen Anne E J, Hruzova Martina, Rothgangl Tanja, Breur Marjolein, Bugiani Marianna, van der Knaap Marjo S, Schwank Gerald, Heine Vivi M

Replacing the SpCas9 HNH domain by deaminases generates compact base editors with an alternative targeting scope

用脱氨酶替换 SpCas9 的 HNH 结构域可生成具有不同靶向范围的紧凑型碱基编辑器

Villiger, Lukas; Schmidheini, Lukas; Mathis, Nicolas; Rothgangl, Tanja; Marquart, Kim; Schwank, Gerald