Severe inflammation and lineage skewing are associated with poor engraftment of engineered hematopoietic stem cells in patients with sickle cell disease
严重的炎症和谱系偏倚与镰状细胞病患者体内工程化造血干细胞移植失败有关。
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-025-58321-4.
Steicy Sobrino ,Laure Joseph ,Elisa Magrin ,Anne Chalumeau ,Nicolas Hebert ,Alice Corsia ,Adeline Denis ,Cécile Roudaut ,Clotilde Aussel ,Olivia Leblanc ,Mégane Brusson ,Tristan Felix ,Jean-Sebastien Diana ,Angelina Petrichenko ,Jana El Etri ,Auria Godard ,Eden Tibi ,Sandra Manceau ,Jean Marc Treluyer ,Fulvio Mavilio ,Frederic D Bushman ,Ambroise Marcais ,Martin Castelle ,Benedicte Neven ,Olivier Hermine ,Sylvain Renolleau ,Alessandra Magnani ,Vahid Asnafi ,Wassim El Nemer ,Pablo Bartolucci ,Emmanuelle Six ,Michaela Semeraro ,Annarita Miccio ,Marina Cavazzana