Ribosomal frameshifting selectively modulates the assembly, function, and pharmacological rescue of a misfolded CFTR variant.
核糖体移码选择性地调节错误折叠的 CFTR 变体的组装、功能和药理学拯救
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:9.1
doi:10.1073/pnas.2414768121
Carmody Patrick J, Roushar Francis J, Tedman Austin, Wang Wei, Herwig Madeline, Kim Minsoo, McDonald Eli F, Noguera Karen, Wong-Roushar Jennifer, Poirier Jon-Luc, Zelt Nathan B, Pockrass Ben T, McKee Andrew G, Kuntz Charles P, Raju S Vamsee, Plate Lars, Penn Wesley D, Schlebach Jonathan P