Transient photoreceptor deconstruction by CNTF enhances rAAV-mediated cone functional rescue in late stage CNGB3-achromatopsia
CNTF介导的瞬时感光细胞解体增强了rAAV介导的视锥细胞功能恢复,从而改善晚期CNGB3致全色盲。
期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2013.50
Komáromy, András M; Rowlan, Jessica S; Corr, Amanda T Parton; Reinstein, Shelby L; Boye, Sanford L; Cooper, Ann E; Gonzalez, Amaliris; Levy, Britt; Wen, Rong; Hauswirth, William W; Beltran, William A; Aguirre, Gustavo D