日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Longitudinal imaging of therapeutic enzyme expression after gene therapy for Fabry disease using positron emission tomography and the radiotracer [(18)F]AGAL

利用正电子发射断层扫描和放射性示踪剂[(18)F]AGAL对法布里病基因治疗后治疗性酶的表达进行纵向成像

Kaittanis, Charalambos; Teceno, Tyler; Knight, Ashley; Petibon, Yoann; Sandoval, Phil; Cohen, Lawrence; Ahn, Shin Hye; Belanger, Anthony P; Clark, Louise M; Nguyen, Quang-De; Ruangsiriluk, Wanida; Mukherji, Shreya; Constantinescu, Cristian C; Amenta, Amy Llopis; Narayanan, Sarav; Deshpande, Mugdha; Islam, Rizwana; Yuan, Shipeng; McQuade, Paul; Winkelmann, Christopher T; Lohith, Talakad G

Reversing Pathology in an Aggravated Fabry Mouse Model Using Low-Dose Engineered Human Alpha-Galactosidase A AAV Gene Therapy.

利用低剂量工程化人α-半乳糖苷酶A AAV基因疗法逆转加重型法布里病小鼠模型的病理变化

Ruangsiriluk Wanida, Deshpande Mugdha, Boukharov Natalia, Rajarshi Girija, Mukherji Shreya, Yuan Shipeng, Wiseman Jennifer, Chen Nancy, Park Eric, Cho Hyelim, Islam Rizwana

Volumetric MRI of dorsal root ganglia as a biomarker for disease progression and response to AAV treatment in a mouse model of Fabry disease.

在法布里病小鼠模型中,背根神经节的体积磁共振成像可作为疾病进展和对 AAV 治疗反应的生物标志物。

Zhao Fuqiang, Yuan Shipeng, Kaittanis Charalambos, Deshpande Mugdha, Kugadas Abirami, Derakhchan Katayoun, Ruangsiriluk Wanida, Islam Rizwana, Boukharov Natalia, McQuade Paul, Tauscher Johannes, Winkelmann Christopher T, Lohith Talakad G

Cardiac manifestations of Fabry disease in G3Stg/GlaKO and GlaKO mouse models-Translation to Fabry disease patients

G3Stg/GlaKO 和 GlaKO 小鼠模型中法布里病的心脏表现——向法布里病患者的转化

Kugadas, Abirami; Artoni, Pietro; Ruangsiriluk, Wanida; Zhao, Meng; Boukharov, Natalia; Islam, Rizwana; Volfson, Dmitri; Derakhchan, Katayoun

Radiosynthesis and Early Evaluation of a Positron Emission Tomography Imaging Probe [18F]AGAL Targeting Alpha-Galactosidase A Enzyme for Fabry Disease

针对法布里病的 α-半乳糖苷酶 A 的正电子发射断层扫描成像探针 [18F]AGAL 的放射合成和早期评估

Talakad G Lohith, Charalambos Kaittanis, Anthony P Belanger, Shin Hye Ahn, Phil Sandoval, Lawrence Cohen, Girija Rajarshi, Wanida Ruangsiriluk, Rizwana Islam, Christopher T Winkelmann, Paul McQuade