日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sustained Correction of a Murine Model of Phenylketonuria following a Single Intravenous Administration of AAVHSC15-PAH

单次静脉注射AAVHSC15-PAH后,苯丙酮尿症小鼠模型得到持续纠正

Ahmed, Seemin S; Rubin, Hillard; Wang, Minglun; Faulkner, Deiby; Sengooba, Arnold; Dollive, Serena N; Avila, Nancy; Ellsworth, Jeff L; Lamppu, Diana; Lobikin, Maria; Lotterhand, Jason; Adamson-Small, Laura; Wright, Teresa; Seymour, Albert; Francone, Omar L

Stem cell-derived clade F AAVs mediate high-efficiency homologous recombination-based genome editing

干细胞衍生的F亚型腺相关病毒(AAV)介导高效的基于同源重组的基因组编辑

Smith, Laura J; Wright, Jason; Clark, Gabriella; Ul-Hasan, Taihra; Jin, Xiangyang; Fong, Abigail; Chandra, Manasa; St Martin, Thia; Rubin, Hillard; Knowlton, David; Ellsworth, Jeff L; Fong, Yuman; Wong, Kamehameha K Jr; Chatterjee, Saswati

Aurintricarboxylic acid increases yield of HSV-1 vectors

金精三羧酸可提高HSV-1载体的产量

Pechan, Peter; Ardinger, Jeffery; Ketavarapu, Jyothi; Rubin, Hillard; Wadsworth, Samuel C; Scaria, Abraham

Inhibition of choroidal neovascularization in a nonhuman primate model by intravitreal administration of an AAV2 vector expressing a novel anti-VEGF molecule.

在非人灵长类动物模型中,通过玻璃体内注射表达新型抗 VEGF 分子的 AAV2 载体抑制脉络膜新生血管形成

Lukason Michael, DuFresne Elizabeth, Rubin Hillard, Pechan Peter, Li Qiuhong, Kim Ivana, Kiss Szilard, Flaxel Christina, Collins Margaret, Miller Joan, Hauswirth William, Maclachlan Timothy, Wadsworth Samuel, Scaria Abraham