A Single Administration of CRISPR/Cas9 Lipid Nanoparticles Achieves Robust and Persistent In Vivo Genome Editing
一次施用 CRISPR/Cas9 脂质纳米粒子即可实现稳健且持久的体内基因组编辑
期刊:Cell Reports
影响因子:7.5
doi:10.1016/j.celrep.2018.02.014
Jonathan D Finn, Amy Rhoden Smith, Mihir C Patel, Lucinda Shaw, Madeleine R Youniss, Jane van Heteren, Tanner Dirstine, Corey Ciullo, Reynald Lescarbeau, Jessica Seitzer, Ruchi R Shah, Aalok Shah, Dandan Ling, Jacqueline Growe, Melissa Pink, Ellen Rohde, Kristy M Wood, William E Salomon, William F H