Effect of Nitisinone on Aortic Stenosis Disease Progression in Patients With Alkaptonuria: An Analysis of the Suitability of Nitisinone in Alkaptonuria (SONIA) 2 Study
尼替西酮对伴有尿黑酸症患者主动脉瓣狭窄疾病进展的影响:尼替西酮在尿黑酸症中适用性分析(SONIA 2 研究)
期刊:Cureus Journal of Medical Science
影响因子:1.3
doi:10.7759/cureus.100123
Bruce, Callum; Meenamkuzhy-Hariharan, Priyanka; Hussain, Shahdat; Eleuteri, Antonio; Ranganath, Lakshminarayan; Fisher, Michael; Imrich, Richard; Arnoux, Jean-Baptiste; Olsson, Birgitta; Rudebeck, Mattias